Targeted gene transfer into ependymal cells through intraventricular injection of AAV1 vector and long-term enzyme replacement via the CSF

Scientific Reports

Volumn 4, Issue , 2014, Pages

  Yamazaki, Yoshiyuki ^a   Hirai, Yukihiko ^a   Miyake, Koichi ^a   Shimada, Takashi ^a  

^a NIPPON MEDICAL SCHOOL   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

CEREBROSIDE SULFATASE;

ADENOVIRIDAE; ANIMAL; C57BL MOUSE; CEREBROSPINAL FLUID; CYTOLOGY; EPENDYMA; GENE TARGETING; GENE VECTOR; GENETIC TRANSFECTION; GENETICS; INTRACEREBROVENTRICULAR DRUG ADMINISTRATION; LONGITUDINAL STUDY; MOUSE; PHYSIOLOGY; PROCEDURES;

ADENOVIRIDAE; ANIMALS; CEREBROSIDE-SULFATASE; EPENDYMA; GENE TARGETING; GENETIC VECTORS; INJECTIONS, INTRAVENTRICULAR; LONGITUDINAL STUDIES; MICE; MICE, INBRED C57BL; TRANSFECTION;

EID: 84903729586     PISSN: None     EISSN: 20452322     Source Type: Journal    
DOI: 10.1038/srep05506     Document Type: Article

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