Personalised medicine in cystic fibrosis must be made affordable

Paediatric Respiratory Reviews

Volumn 15, Issue S1, 2014, Pages 6-7

  Bilton, Diana ^a  

^a ROYAL BROMPTON HOSPITAL   (United Kingdom)

Author keywords

Cystic Fibrosis; Personalised Medicine

Indexed keywords

ANTIBIOTIC AGENT; ASPARTIC ACID; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; GLYCINE; IVACAFTOR;

AFFORDABILITY; ARTICLE; BUDGET; CLINICAL RESEARCH; CONFIDENTIALITY; COST EFFECTIVENESS ANALYSIS; CROSS INFECTION; CYSTIC FIBROSIS; DISEASE EXACERBATION; DISEASE REGISTRY; DRUG APPROVAL; DRUG COST; DRUG EFFICACY; EVIDENCE BASED MEDICINE; FINANCIAL MANAGEMENT; FORCED EXPIRATORY VOLUME; FUNDING; GENE MUTATION; HEALTH CARE; HEALTH CARE ACCESS; HEALTH CARE COST; HEALTH CARE DELIVERY; HEALTH CARE PLANNING; HEALTH CARE QUALITY; HEALTH CARE SYSTEM; HEALTH INSURANCE; HEALTH SERVICE; HOME CARE; HUMAN; INFECTION RISK; ION TRANSPORT; LUNG CLEARANCE; LUNG INFECTION; MEDICAL SPECIALIST; NEBULIZATION; PATIENT ATTITUDE; PATIENT CARE; PATIENT MONITORING; PERSONALIZED MEDICINE; PRIORITY JOURNAL; TABLET; TEAMWORK; ADULT; CHILD; COST; ECONOMICS;

ADULT; CHILD; COSTS AND COST ANALYSIS; CYSTIC FIBROSIS; HUMANS; INDIVIDUALIZED MEDICINE;

EID: 84901589330     PISSN: 15260542     EISSN: 15260550     Source Type: Journal    
DOI: 10.1016/j.prrv.2014.04.004     Document Type: Article

References (4)

1. Ramsey B.W., Davies J., McElvaney N.G., et al. A CFTR potentiator in patients with cystic fibrosis and the G551D mutation. N Engl J Med 2011, 365:1663-1672.
2. Riordan J.R., Rommens J.M., Kerem B., et al. Identification of the cystic fibrosis gene: cloning and characterization of complementary DNA. Science 1989, 245:1066-1073.
3. Sawicki G.S., Walter D.E., Robinson M. High treatment burden in adults with cystic fibrosis: challenges to disease self-management. J Cyst Fibros. 2009, 8(2):91-96.
4. Davies J.C., Wainwright C.E., Canny G.J., et al. Efficacy and safety of ivacaftor in patients aged 6 to 11 years with cystic fibrosis with a G551D mutation. Am J Resp Crit Care Med 2013, 187:1219-1225.