Biodistribution of AAV8 vectors expressing human low-density lipoprotein receptor in a mouse model of homozygous familial hypercholesterolemia

Human Gene Therapy Clinical Development

Volumn 24, Issue 4, 2013, Pages 154-160

  Chen, Shu Jen ^a   Sanmiguel, Julio ^a   Lock, Martin ^a   McMenamin, Deirdre ^a   Draper, Christine ^a   Limberis, Maria P ^a   Kassim, Sadik H ^a,b   Somanathan, Suryanarayan ^a   Bell, Peter ^a   Johnston, Julie C ^a   Rader, Daniel J ^a   Wilson, James M ^a  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b NATIONAL CANCER INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

LOW DENSITY LIPOPROTEIN RECEPTOR; PARVOVIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONTROLLED STUDY; FAMILIAL HYPERCHOLESTEROLEMIA; FEMALE; MALE; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; VIRAL GENE THERAPY; VIRUS GENOME;

ANIMALS; CHOLESTEROL; CLINICAL TRIALS AS TOPIC; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; FEMALE; GENETIC THERAPY; GENETIC VECTORS; HOMOZYGOTE; HUMANS; HYPERLIPOPROTEINEMIA TYPE II; MALE; MICE; RECEPTORS, LDL; TIME FACTORS; TISSUE DISTRIBUTION;

EID: 84901447384     PISSN: 23248637     EISSN: 23248645     Source Type: Journal    
DOI: 10.1089/humc.2013.082     Document Type: Article

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