EIAV-based retinal gene therapy in the shaker1 mouse model for usher syndrome type 1B: Development of UshStat

PLoS ONE

Volumn 9, Issue 4, 2014, Pages

  Zallocchi, Marisa ^a   Binley, Katie ^b   Lad, Yatish ^b   Ellis, Scott ^b   Widdowson, Peter ^b   Iqball, Sharifah ^b   Scripps, Vicky ^b   Kelleher, Michelle ^b   Loader, Julie ^b   Miskin, James ^b   Peng, You Wei ^a   Wang, Wei Min ^a   Cheung, Linda ^a   Delimont, Duane ^a   Mitrophanous, Kyriacos A ^b   Cosgrove, Dominic ^a,c  

^a BOYS TOWN NATIONAL RESEARCH HOSPITAL   (United States)

^b OXFORD BIOMEDICA UK LTD   (United Kingdom)

^c UNIVERSITY OF NEBRASKA MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA TRANSDUCIN; GREEN FLUORESCENT PROTEIN; LENTIVIRUS VECTOR; MYOSIN VIIA; TRANSDUCIN; UNCLASSIFIED DRUG; USHSTAT; MYOSIN;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DRUG TOLERABILITY; EQUINE INFECTIOUS ANEMIA VIRUS; EQUINE INFECTIOUS ANEMIA VIRUS BASED RETINAL GENE THERAPY; FEMALE; HISTOLOGY; HUMORAL IMMUNITY; HYPERPIGMENTATION; HYPERPLASIA; HYPERTROPHY; MALE; MOUSE; NERVE FIBER DEGENERATION; NEWBORN; NONHUMAN; PHENOTYPE; PHOTORECEPTOR INNER SEGMENT; PHOTORECEPTOR OUTER SEGMENT; PIGMENT EPITHELIUM; PROTEIN EXPRESSION; RETINA DEGENERATION; RETINA EDEMA; RHESUS MONKEY; SAFETY; TRANSGENE; USHER SYNDROME; VIRAL GENE THERAPY; ADMINISTRATION AND DOSAGE; ANIMAL; CELL LINE; DISEASE MODEL; GENE ORDER; GENE THERAPY; GENE VECTOR; GENETICS; HUMAN; KNOCKOUT MOUSE; MACACA; METABOLISM; PATHOLOGY; PHOTORECEPTOR CELL; PROTEIN TRANSPORT; RETINA; USHER SYNDROMES;

ANIMALS; CELL LINE; DISEASE MODELS, ANIMAL; FEMALE; GENE ORDER; GENETIC THERAPY; GENETIC VECTORS; HUMANS; INFECTIOUS ANEMIA VIRUS, EQUINE; MACACA; MALE; MICE; MICE, KNOCKOUT; MYOSINS; PHENOTYPE; PHOTORECEPTOR CELLS; PROTEIN TRANSPORT; RETINA; TRANSDUCIN; USHER SYNDROMES;

EID: 84899069485     PISSN: None     EISSN: 19326203     Source Type: Journal    
DOI: 10.1371/journal.pone.0094272     Document Type: Article

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