SCOPUS 정보 검색 플랫폼

Volumn 123, Issue 12, 2014, Pages 1956-1957

A phase 2 trial of HQK-1001 in HbE-β thalassemia demonstrates HbF induction and reduced anemia

(7) Patthamalai, Poramin a Fuchareon, Suthat a Chaneiam, Nattawara a Ghalie, Richard G b Chui, David H K c Boosalis, Michael S c Perrine, Susan P c

a MAHIDOL UNIVERSITY (Thailand)

b HemaQuest Pharmaceuticals (United States)

c BOSTON UNIVERSITY SCHOOL OF MEDICINE (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ANTIANEMIC AGENT; HEMOGLOBIN E; HEMOGLOBIN F; HQK 1001; SHORT CHAIN FATTY ACID; SODIUM 2,2 DIMETHYLBUYRATE; SODIUM DERIVATIVE; UNCLASSIFIED DRUG;

BETA THALASSEMIA; DRUG EFFICACY; DRUG SAFETY; DRUG TOLERABILITY; GENE MUTATION; HEMOGLOBIN BLOOD LEVEL; HUMAN; LETTER; PHASE 2 CLINICAL TRIAL (TOPIC); PRIORITY JOURNAL; PROTEIN INDUCTION;

ADULT; BETA-THALASSEMIA; BUTYRATES; FEMALE; FETAL HEMOGLOBIN; HEMOGLOBIN E; HEMOGLOBINS; HUMANS; MALE; YOUNG ADULT;

EID: 84897487469 PISSN: 00064971 EISSN: 15280020 Source Type: Journal
DOI: 10.1182/blood-2013-11-538470 Document Type: Letter

Times cited : (18)

References (10)

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