Emerging therapy in hemoglobinopathies: Lessons from the past and optimism for the future

Hematology/Oncology Clinics of North America

Volumn 28, Issue 2, 2014, Pages

  Vichinsky, Elliott P ^a  

^a CHILDREN S HOSPITAL OAKLAND   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

5 AZA 2' DEOXYCYTIDINE; ANTISENSE OLIGONUCLEOTIDE; AZACITIDINE; BENSERAZIDE; CETIEDIL; HEMOGLOBIN; HEMOGLOBIN F; HEPCIDIN; HISTONE DEACETYLASE INHIBITOR; HYDROXYUREA; LUSPATERCEPT; RIVIPANSEL; SMALL INTERFERING RNA; TETRAHYDROURIDINE; TRANSFERRIN;

ANTISENSE THERAPY; EDITORIAL; ERYTHROPOIESIS; FOOD AND DRUG ADMINISTRATION; HEMOGLOBINOPATHY; HISTORY OF MEDICINE; HUMAN; IRON OVERLOAD; NONHUMAN; OXYGEN AFFINITY; PATHOPHYSIOLOGY; PRIORITY JOURNAL; SICKLE CELL ANEMIA; THALASSEMIA; THALASSEMIA INTERMEDIA; VASCULAR DISEASE; FORECASTING; GENE THERAPY; GENETICS; HEMOGLOBINOPATHIES; MOLECULARLY TARGETED THERAPY; PROCEDURES; TRENDS;

FORECASTING; GENETIC THERAPY; HEMOGLOBINOPATHIES; HUMANS; MOLECULAR TARGETED THERAPY;

EID: 84896718597     PISSN: 08898588     EISSN: 15581977     Source Type: Journal    
DOI: 10.1016/j.hoc.2014.01.001     Document Type: Editorial

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