Single centre experience of haematopoietic SCT for patients with immunodysregulation, polyendocrinopathy, enteropathy, X-linked syndrome

Bone Marrow Transplantation

Volumn 49, Issue 2, 2014, Pages 310-312

  Nademi, Z ^a,b   Slatter, M ^a,b   Gambineri, E ^c   Mannurita, S C ^c   Barge, D ^d   Hodges, S ^d   Bunn, S ^d   Thomas, J ^d   Haugk, B ^d   Hambleton, S ^a,b   Flood, T ^a   Cant, A ^a,b   Abinun, M ^a,b   Gennery, A ^a,b  

^a Newcastle Upon Tyne   (Italy)

^b NEWCASTLE UNIVERSITY   (United Kingdom)

^c Hematology Department   (Italy)

^d NEWCASTLE UPON TYNE HOSPITALS NHS FOUNDATION TRUST   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

DIARRHEA; GENETIC DISEASES, X-LINKED; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; IMMUNOLOGIC DEFICIENCY SYNDROMES; INFANT; INFANT, NEWBORN; POLYENDOCRINOPATHIES, AUTOIMMUNE; TRANSPLANTATION CONDITIONING;

EID: 84893739675     PISSN: 02683369     EISSN: 14765365     Source Type: Journal    
DOI: 10.1038/bmt.2013.181     Document Type: Letter

References (10)

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2. Gambineri E, Perroni L, Passerini L, Bianchi L, Doglioni C, Meschi F et al. Clinical and molecular profile of a new series of patients with immune dysregulation, polyendocrinopathy, enteropathy, X-linked syndrome: inconsistent correlation between forkhead box protein 3 expression and disease severity. J Allergy Clin Immunol 2008; 122: 1105-1112.
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