AAV-mediated gene delivery in Dp71-null mouse model with compromised barriers

GLIA

Volumn 62, Issue 3, 2014, Pages 468-476

  Vacca, Ophélie ^a   Darche, Marie ^a   Schaffer, David V ^b   Flannery, John G ^b   Sahel, José Alain ^a,c,d,e   Rendon, Alvaro ^a   Dalkara, Deniz ^a  

^a CENTRE HOSPITALIER NATIONAL D OPHTALMOLOGIE DES QUINZE VINGTS   (France)

^b UNIVERSITY OF CALIFORNIA   (United States)

^c FONDATION OPHTALMOLOGIQUE ADOLPHE DE ROTHSCHILD   (France)

^d UNIVERSITY COLLEGE LONDON   (United Kingdom)

^e Académie des Sciences Institut de France Paris   (France)

Author keywords

AAV; Blood retinal barrier; Dystrophin Dp71; Inner limiting membrane; M ller cell

Indexed keywords

DYSTROPHIN; DYSTROPHIN 71; GREEN FLUORESCENT PROTEIN; LAMININ; UNCLASSIFIED DRUG; APO-DYSTROPHIN 1;

ADENO ASSOCIATED VIRUS; ANIMAL CELL; ANIMAL EXPERIMENT; ARTICLE; ASTROCYTE; BLOOD RETINA BARRIER; CELL MEMBRANE; CELL MEMBRANE PERMEABILITY; CELL SPECIFICITY; CELL STRUCTURE; CONTROLLED STUDY; GENETIC CODE; GLIA CELL; INNER LIMITING MEMBRANE; MOUSE; MUELLER CELL; NONHUMAN; PHOTORECEPTOR CELL; PRIORITY JOURNAL; RETINAL THICKNESS; SEROTYPE; VIRAL GENE THERAPY; ADENOVIRIDAE; ANIMAL; DEFICIENCY; DISEASE MODEL; EYE FUNDUS; GENE TRANSFER; GENETICS; KNOCKOUT MOUSE; MACROGLIA; METABOLISM; OPTICAL COHERENCE TOMOGRAPHY; PATHOLOGY; PATHOPHYSIOLOGY; RETINA; RETINA DISEASE; VISUAL SYSTEM;

ADENOVIRIDAE; ANIMALS; BLOOD-RETINAL BARRIER; DISEASE MODELS, ANIMAL; DYSTROPHIN; EPENDYMOGLIAL CELLS; FUNDUS OCULI; GENE TRANSFER TECHNIQUES; GREEN FLUORESCENT PROTEINS; MICE; MICE, KNOCKOUT; PHOTORECEPTOR CELLS; RETINA; RETINAL DISEASES; TOMOGRAPHY, OPTICAL COHERENCE; VISUAL PATHWAYS;

EID: 84892503259     PISSN: 08941491     EISSN: 10981136     Source Type: Journal    
DOI: 10.1002/glia.22617     Document Type: Article

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