DMD transcript imbalance determines dystrophin levels

FASEB Journal

Volumn 27, Issue 12, 2013, Pages 4909-4916

  Spitali, Pietro ^a   Van Den Bergen, Janneke C ^a   Verhaart, Ingrid E C ^a   Wokke, Beatrijs ^a   Janson, Anneke A M ^b   Van Den Eijnde, Rani ^b   Den Dunnen, Johan T ^a   Laros, Jeroen F J ^a   Verschuuren, Jan J G M ^a   C 't Hoen, Peter A ^a   Aartsma Rus, Annemieke ^a  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

^b Prosensa Therapeutics   (Netherlands)

Author keywords

Antisense oligonucleotides; Duchenne muscular dystrophy; Exon skipping; Transcript stability

Indexed keywords

DYSTROPHIN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BECKER MUSCULAR DYSTROPHY; DUCHENNE MUSCULAR DYSTROPHY GENE; EXON; GENE; GENE EXPRESSION; HEART MUSCLE; MOUSE; NONHUMAN; NONSENSE MUTATION; PRIORITY JOURNAL; SKELETAL MUSCLE;

ANTISENSE OLIGONUCLEOTIDES; DUCHENNE MUSCULAR DYSTROPHY; EXON SKIPPING; TRANSCRIPT STABILITY;

3' UNTRANSLATED REGIONS; 5' UNTRANSLATED REGIONS; ANIMALS; CODON, NONSENSE; DYSTROPHIN; ECTHYMA, CONTAGIOUS; EXONS; HUMANS; MICE; MICE, INBRED MDX; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE; MYOCARDIUM; NONSENSE MEDIATED MRNA DECAY; RNA, MESSENGER; TRANSCRIPTION, GENETIC;

EID: 84890456939     PISSN: None     EISSN: 15306860     Source Type: Journal    
DOI: 10.1096/fj.13-232025     Document Type: Article

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