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Volumn 13, Issue 3, 2013, Pages 263-264
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Broadening the indications for hematopoietic stem cell genetic therapies
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Author keywords
[No Author keywords available]
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Indexed keywords
COMPLEMENTARY DNA;
LENTIVIRUS VECTOR;
MEMBRANE PROTEIN;
RETROVIRUS VECTOR;
UNCLASSIFIED DRUG;
VIRUS VECTOR;
WAS PROTEIN;
ADENOSINE DEAMINASE DEFICIENCY;
CEREBROSPINAL FLUID;
CHIMERA;
COGNITIVE DEFECT;
DEMYELINATION;
GENE THERAPY;
GENE TRANSFER;
GENOTOXICITY;
HEMATOPOIETIC STEM CELL;
HEMATOPOIETIC STEM CELL TRANSPLANTATION;
HUMAN;
IMMUNE DEFICIENCY;
LEUKEMIA;
LYMPHOMA;
LYSOSOME STORAGE DISEASE;
METACHROMATIC LEUKODYSTROPHY;
MICROGLIA;
MUTAGENESIS;
MYELODYSPLASTIC SYNDROME;
PRELEUKEMIA;
PRIORITY JOURNAL;
PROGENY;
PROTEIN EXPRESSION;
RARE DISEASE;
SHORT SURVEY;
SOMATIC CELL;
STEM CELL;
TARGET CELL;
THROMBOCYTE;
THROMBOCYTE COUNT;
TRANSACTIVATION;
TRANSGENE;
TREATMENT INDICATION;
VIRAL GENE DELIVERY SYSTEM;
VIRAL GENE THERAPY;
WISKOTT ALDRICH SYNDROME;
X LINKED SEVERE COMBINED IMMUNODEFICIENCY;
CEREBROSIDE-SULFATASE;
GENETIC THERAPY;
HEMATOPOIETIC STEM CELL TRANSPLANTATION;
HEMATOPOIETIC STEM CELLS;
HUMANS;
LEUKODYSTROPHY, METACHROMATIC;
MALE;
WISKOTT-ALDRICH SYNDROME;
WISKOTT-ALDRICH SYNDROME PROTEIN;
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EID: 84884162833
PISSN: 19345909
EISSN: 18759777
Source Type: Journal
DOI: 10.1016/j.stem.2013.08.006 Document Type: Short Survey |
Times cited : (12)
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References (9)
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