Lentiviral gene transfer of TCIRG1 into peripheral blood CD34+ cells restores osteoclast function in infantile malignant osteopetrosis

Bone

Volumn 57, Issue 1, 2013, Pages 1-9

  Moscatelli, Ilana ^a   Thudium, Christian Schneider ^a,b   Flores, Carmen ^a   Schulz, Ansgar ^c   Askmyr, Maria ^a   Gudmann, Natasja Stæhr ^b   Andersen, Nanna Merete ^b   Porras, Oscar ^d   Karsdal, Morten Asser ^b   Villa, Anna ^e,f   Fasth, Anders ^g   Henriksen, Kim ^b   Richter, Johan ^a  

^a Lund Strategic Center for Stem Cell Biology   (Sweden)

^b NORDIC BIOSCIENCE A S   (Denmark)

^c UNIVERSITY HOSPITAL ULM   (Germany)

^d National Children's Hospital   (Costa Rica)

^e CNR   (Italy)

^f HUMANITAS CLINICAL AND RESEARCH CENTER   (Italy)

^g UNIVERSITY OF GOTHENBURG   (Sweden)

Author keywords

Hematopoietic stem cells; Infantile malignant osteopetrosis; Lentiviral gene transfer; Osteoclasts; TCIRG1

Indexed keywords

ADENOSINE TRIPHOSPHATASE; CARBOXY TERMINAL TELOPEPTIDE; CD34 ANTIGEN; LENTIVIRUS VECTOR; MESSENGER RNA; PROTON PUMP; UNCLASSIFIED DRUG; VACUOLAR ADENOSINE TRIPHOSPHATASE PROTON PUMP SUBUNIT A3;

ALBERS SCHOENBERG DISEASE; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CHILD; CLINICAL ARTICLE; CONTROLLED STUDY; FEMALE; HUMAN; HUMAN CELL; HUMAN TISSUE; INFANT; INFANTILE MALIGNANT OSTEOPETROSIS; MALE; MOUSE; NONHUMAN; NUCLEOTIDE SEQUENCE; OSTEOCLAST; PERIPHERAL BLOOD MONONUCLEAR CELL; POLYMERASE CHAIN REACTION; PROTEIN EXPRESSION; TCIRG1 GENE; WESTERN BLOTTING;

HEMATOPOIETIC STEM CELLS; INFANTILE MALIGNANT OSTEOPETROSIS; LENTIVIRAL GENE TRANSFER; OSTEOCLASTS; TCIRG1;

ANIMALS; ANTIGENS, CD34; CELLS, CULTURED; CHILD; CHILD, PRESCHOOL; FEMALE; FLOW CYTOMETRY; HUMANS; IMMUNOBLOTTING; INFANT; INFANT, NEWBORN; LENTIVIRUS; MALE; MICE; MICE, SCID; OSTEOCLASTS; OSTEOPETROSIS; POLYMERASE CHAIN REACTION; VACUOLAR PROTON-TRANSLOCATING ATPASES;

EID: 84882696526     PISSN: 87563282     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.bone.2013.07.026     Document Type: Article

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