Choroideremia: Towards a therapy

American Journal of Ophthalmology

Volumn 156, Issue 3, 2013, Pages

  Kalatzis, Vasiliki ^a   Hamel, Christian P ^a   Macdonald, Ian M ^b  

^a Montpellier University Medical Center   (France)

^b UNIVERSITY OF ALBERTA   (Canada)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; CHM PROTEIN; ELONGATION FACTOR 1; LENTIVIRUS VECTOR; MEMBRANE PROTEIN; MESSENGER RNA; PLASMID VECTOR; UNCLASSIFIED DRUG;

ABSENCE OF SIDE EFFECTS; ADENO ASSOCIATED VIRUS; ARTICLE; AUTOFLUORESCENCE; CELL ACTIVATION; CHOROID; CHOROID CAPILLARY LAYER; CHOROID VASCULARIZATION; CHOROIDEREMIA; CLINICAL EFFECTIVENESS; CLINICAL TRIAL (TOPIC); CYTOMEGALOVIRUS; DISEASE COURSE; DNA BINDING MOTIF; DRUG DELIVERY SYSTEM; EXON; GENE THERAPY; GENE TRANSFER; GENETIC COUNSELING; GENETIC VARIABILITY; HUMAN; HUMAN ADENOVIRUS; INVERTED TERMINAL REPEAT; LEBER CONGENITAL AMAUROSIS; MEDICAL LITERATURE; MUTATIONAL ANALYSIS; PATHOPHYSIOLOGY; PERIPHERAL VISION; PHENOTYPE; PHOTORECEPTOR; PHOTORECEPTOR CELL; PIGMENT EPITHELIUM; PRIORITY JOURNAL; PROMOTER REGION; RETINA DETACHMENT; RETINA DYSTROPHY; TRANSGENE; TROPISM; VIRAL GENE THERAPY; VISUAL IMPAIRMENT; X CHROMOSOME INACTIVATION;

EID: 84882249281     PISSN: 00029394     EISSN: 18791891     Source Type: Journal    
DOI: 10.1016/j.ajo.2013.05.009     Document Type: Article

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