Liver transplantation and cell therapies for inborn errors of metabolism

Journal of Inherited Metabolic Disease

Volumn 36, Issue 4, 2013, Pages 675-680

  McKiernan, Patrick ^a  

^a BIRMINGHAM CHILDREN S HOSPITAL   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENT FACTOR H; COMPLEMENT FACTOR I; DNA DIRECTED DNA POLYMERASE GAMMA; ECULIZUMAB; GRANULOCYTE COLONY STIMULATING FACTOR; OXALIC ACID;

CLINICAL EFFECTIVENESS; CONFERENCE PAPER; CONTROLLED CLINICAL TRIAL (TOPIC); DISEASE SEVERITY; GLYCOGEN STORAGE DISEASE TYPE 1; HEMOLYTIC UREMIC SYNDROME; HEPATOCYTE TRANSPLANTATION; HETEROZYGOTE; HUMAN; INBORN ERROR OF METABOLISM; LIVER DISEASE; LIVER FAILURE; LIVER TRANSPLANTATION; LIVING DONOR; LONG TERM SURVIVAL; OXALOSIS 1; PATIENT SAFETY; STEM CELL TRANSPLANTATION; TREATMENT OUTCOME; UREA CYCLE DISORDER;

CELL- AND TISSUE-BASED THERAPY; HUMANS; LIVER TRANSPLANTATION; METABOLIC DISEASES; METABOLISM, INBORN ERRORS; STEM CELL TRANSPLANTATION; STEM CELLS;

EID: 84880212541     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-012-9581-z     Document Type: Conference Paper

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