Arginine butyrate: A therapeutic candidate for Duchenne muscular dystrophy

FASEB Journal

Volumn 27, Issue 6, 2013, Pages 2256-2269

  Vianello, Sara ^a   Yu, Hua ^a   Voisin, Vincent ^a   Haddad, Hafedh ^a   He, Xun ^a   Foutz, Arthur S ^a   Sebrié, Catherine ^a   Gillet, Brigitte ^a   Roulot, Morgane ^a   Fougerousse, Françoise ^b   Perronnet, Caroline ^c,d,h   Vaillend, Cyrille ^c,d   Matecki, Stefan ^e   Escolar, Diana ^f   Bossi, Laura ^g   Israël, Maurice ^a   De La Porte, Sabine ^a  

^a CNRS   (France)

^b GÉNÉTHON   (France)

^c UNIVERSITÉ PARIS SACLAY   (France)

^d INSTITUT D'OPTIQUE GRADUATE SCHOOL   (France)

^e UNIV MONTPELLIER   (France)

^f JOHNS HOPKINS UNIVERSITY SCHOOL OF MEDICINE   (United States)

^g Domain Therapeutics   (France)

^h UNIVERSITY OF BRITISH COLUMBIA   (Canada)

Author keywords

DMD; Histone deacetylase; Mdx; NO; Pharmacology; Treatment

Indexed keywords

ARGININE; ARGININE BUTYRATE; BUTYRIC ACID DERIVATIVE; CREATINE KINASE; DYSTROPHIN; HISTONE DEACETYLASE; NITRIC OXIDE; UNCLASSIFIED DRUG; UTROPHIN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BRAIN; CONTROLLED STUDY; DRUG EFFICACY; DRUG SAFETY; DUCHENNE MUSCULAR DYSTROPHY; GRIP STRENGTH; HEART; IN VITRO STUDY; IN VIVO STUDY; MOUSE; MUSCLE NECROSIS; NEWBORN; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; PROTEIN EXPRESSION; SKELETAL MUSCLE; SKIN BIOPSY;

DMD; HISTONE DEACETYLASE; MDX; NO; PHARMACOLOGY; TREATMENT;

ANIMALS; ANIMALS, NEWBORN; ARGININE; BUTYRATES; CELLS, CULTURED; DRUG SYNERGISM; HISTONE DEACETYLASE INHIBITORS; HUMANS; MALE; MICE; MICE, INBRED C57BL; MICE, INBRED MDX; MUSCLE FIBERS, SKELETAL; MUSCULAR DYSTROPHY, ANIMAL; MUSCULAR DYSTROPHY, DUCHENNE; UP-REGULATION; UTROPHIN;

MUS;

EID: 84878756939     PISSN: None     EISSN: 15306860     Source Type: Journal    
DOI: 10.1096/fj.12-215723     Document Type: Article

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