From mutation identification to therapy: Discovery and origins of the first approved gene therapy in the western world

Human Gene Therapy

Volumn 24, Issue 5, 2013, Pages 472-478

  Kastelein, John J P ^a   Ross, Colin J D ^b,c   Hayden, Michael R ^b,c  

^a UNIVERSITY OF AMSTERDAM   (Netherlands)

^b UNIVERSITY OF BRITISH COLUMBIA   (Canada)

^c UNIVERSITY OF BRITISH COLUMBIA   (Canada)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOSINE DEAMINASE; ADENOVIRUS VECTOR; BACULOVIRUS VECTOR; CYCLOSPORIN A; LIPOPROTEIN LIPASE; MYCOPHENOLIC ACID 2 MORPHOLINOETHYL ESTER;

ADENOSINE DEAMINASE DEFICIENCY; DRUG EFFICACY; DRUG SAFETY; GENE MUTATION; GENE THERAPY; HUMAN; HYPERLIPOPROTEINEMIA TYPE 1; HYPERTRIGLYCERIDEMIA; NONHUMAN; NOTE; XANTHOMA;

GENETIC THERAPY; HISTORY, 20TH CENTURY; HUMANS; HYPERLIPOPROTEINEMIA TYPE I; MUTATION; WESTERN WORLD;

EID: 84877856412     PISSN: 10430342     EISSN: 15577422     Source Type: Journal    
DOI: 10.1089/hum.2013.063     Document Type: Note

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