The role of hematopoietic stem cell transplantation in SP110 associated veno-occlusive disease with immunodeficiency syndrome

Pediatric Allergy and Immunology

Volumn 24, Issue 3, 2013, Pages 250-256

  Ganaiem, Hammam ^a   Eisenstein, Eli M ^a   Tenenbaum, Ariel ^a   Somech, Raz ^b   Simanovsky, Natalia ^a   Roscioli, Tony ^c   Weintraub, Michael ^a   Stepensky, Polina ^a  

^a HADASSAH HEBREW UNIVERSITY MEDICAL CENTER   (Israel)

^b Pediatric Immunology Service Jeffery Modell Foundation (JMF) Center   (Israel)

^c UNIVERSITY OF NEW SOUTH WALES   (Australia)

Author keywords

Combined immunodeficiency; Hematopoietic stem cell transplantation; SP110; Veno occlusive disease with immunodeficiency

Indexed keywords

ALEMTUZUMAB; BUSULFAN; CYCLOPHOSPHAMIDE; DEFIBROTIDE; FLUDARABINE; IMMUNOGLOBULIN; IMMUNOGLOBULIN A; IMMUNOGLOBULIN G; IMMUNOGLOBULIN M; MITOGENIC AGENT; THIOTEPA; THYMOCYTE ANTIBODY; TREOSULFAN;

ARTICLE; CHILD; CLINICAL ARTICLE; CLINICAL EFFECTIVENESS; DISEASE COURSE; ETHNICITY; GENE; GENE MUTATION; GENETIC SCREENING; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEPATOSPLENOMEGALY; HUMAN; HUMAN CELL; HUMAN TISSUE; IMMUNOGLOBULIN DEFICIENCY; IMMUNOSUPPRESSIVE TREATMENT; INFANT; LIVER BIOPSY; LIVER INJURY; LIVER VENOOCCLUSIVE DISEASE; PEDIGREE; PRESCHOOL CHILD; PRIORITY JOURNAL; SEVERE COMBINED IMMUNODEFICIENCY; SP110 GENE; VEIN OCCLUSION; VENOOCCLUSIVE DISEASE WITH IMMUNODEFICIENCY;

CHILD, PRESCHOOL; DNA MUTATIONAL ANALYSIS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEPATIC VENO-OCCLUSIVE DISEASE; HUMANS; IMMUNOLOGIC DEFICIENCY SYNDROMES; INFANT; INFANT, NEWBORN; LIVER; MALE; NUCLEAR PROTEINS; TRANSPLANTATION CONDITIONING; TREATMENT OUTCOME;

EID: 84876448639     PISSN: 09056157     EISSN: 13993038     Source Type: Journal    
DOI: 10.1111/pai.12051     Document Type: Article

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