Long circulating enzyme replacement therapy rescues bone pathology in mucopolysaccharidosis VII murine model

Molecular Genetics and Metabolism

Volumn 107, Issue 1-2, 2012, Pages 161-172

  Rowan, Daniel J ^a   Tomatsu, Shunji ^b   Grubb, Jeffrey H ^a   Haupt, Bisong ^a   Montaño, Adriana M ^a   Oikawa, Hirotaka ^a   Sosa, Angela C ^a   Chen, Anping ^a   Sly, William S ^a  

^a SAINT LOUIS UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b NEMOURS ALFRED I DUPONT HOSPITAL FOR CHILDREN   (United States)

Author keywords

Enzyme replacement therapy; Micro CT; Quantitative histopathological assay

Indexed keywords

BETA GLUCURONIDASE;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BONE RADIOGRAPHY; CLINICAL EFFECTIVENESS; CONTROLLED STUDY; ENZYME REPLACEMENT; GROWTH PLATE; HISTOPATHOLOGY; MICRO-COMPUTED TOMOGRAPHY; MOUSE; MUCOPOLYSACCHARIDOSIS TYPE 7; NONHUMAN; PRIORITY JOURNAL; QUANTITATIVE ANALYSIS; TREATMENT OUTCOME;

ANIMALS; BONE DISEASES; CARTILAGE, ARTICULAR; CERVICAL VERTEBRAE; ENZYME REPLACEMENT THERAPY; GLUCURONIDASE; GROWTH PLATE; KNEE JOINT; MICE; MUCOPOLYSACCHARIDOSIS VII; RECOMBINANT PROTEINS; TOMOGRAPHY, X-RAY COMPUTED;

MURINAE; MUS;

EID: 84866184131     PISSN: 10967192     EISSN: 10967206     Source Type: Journal    
DOI: 10.1016/j.ymgme.2012.07.002     Document Type: Article

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