메뉴 건너뛰기




Volumn 10, Issue , 2012, Pages

An acidic oligopeptide displayed on AAV2 improves axial muscle tropism after systemic delivery

Author keywords

Acidic oligopeptide; Adeno associated virus; L aspartic acid; Tropism

Indexed keywords

AMINO ACID; ASPARTIC ACID; ASPARTIC ACID PARVOVIRUS VECTOR 2; OLIGOPEPTIDE; PARVOVIRUS VECTOR; UNCLASSIFIED DRUG;

EID: 84862247520     PISSN: None     EISSN: 14790556     Source Type: Journal    
DOI: 10.1186/1479-0556-10-3     Document Type: Article
Times cited : (5)

References (22)
  • 1
    • 44049094771 scopus 로고    scopus 로고
    • Clinical gene therapy using recombinant adeno-associated virus vectors
    • 10.1038/gt.2008.68, 18418415
    • Mueller C, Flotte TR. Clinical gene therapy using recombinant adeno-associated virus vectors. Gene Ther 2008, 15:858-863. 10.1038/gt.2008.68, 18418415.
    • (2008) Gene Ther , vol.15 , pp. 858-863
    • Mueller, C.1    Flotte, T.R.2
  • 2
    • 0029843596 scopus 로고    scopus 로고
    • Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector
    • 190884, 8892935
    • Xiao X, Li J, Samulski RJ. Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector. J Virol 1996, 70:8098-8108. 190884, 8892935.
    • (1996) J Virol , vol.70 , pp. 8098-8108
    • Xiao, X.1    Li, J.2    Samulski, R.J.3
  • 3
    • 0032853699 scopus 로고    scopus 로고
    • Immune responses to adenovirus and adeno-associated virus in humans
    • 10.1038/sj.gt.3300994, 10490767
    • Chirmule N, Propert K, Magosin S, Qian Y, Qian R, Wilson J. Immune responses to adenovirus and adeno-associated virus in humans. Gene Ther 1999, 6:1574-1583. 10.1038/sj.gt.3300994, 10490767.
    • (1999) Gene Ther , vol.6 , pp. 1574-1583
    • Chirmule, N.1    Propert, K.2    Magosin, S.3    Qian, Y.4    Qian, R.5    Wilson, J.6
  • 4
    • 77956628142 scopus 로고    scopus 로고
    • RH10 provides superior transgene expression in mice when compared with natural AAV serotypes for neonatal gene therapy
    • 10.1002/jgm.1496, 2948027, 20821747
    • Hu C, Busuttil RW, Lipshutz GS. RH10 provides superior transgene expression in mice when compared with natural AAV serotypes for neonatal gene therapy. J Gene Med 2010, 12:766-778. 10.1002/jgm.1496, 2948027, 20821747.
    • (2010) J Gene Med , vol.12 , pp. 766-778
    • Hu, C.1    Busuttil, R.W.2    Lipshutz, G.S.3
  • 5
    • 44349170706 scopus 로고    scopus 로고
    • Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection
    • 10.1038/mt.2008.76, 18414476
    • Zincarelli C, Soltys S, Rengo G, Rabinowitz JE. Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection. Mol Ther 2008, 16:1073-1080. 10.1038/mt.2008.76, 18414476.
    • (2008) Mol Ther , vol.16 , pp. 1073-1080
    • Zincarelli, C.1    Soltys, S.2    Rengo, G.3    Rabinowitz, J.E.4
  • 6
    • 79959201563 scopus 로고    scopus 로고
    • The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9-dependent innate immune responses in the liver
    • 10.1182/blood-2010-10-314518, 3123017, 21474674
    • Martino AT, Suzuki M, Markusic DM, Zolotukhin I, Ryals RC, Moghimi B, Ertl HC, Muruve DA, Lee B, Herzog RW. The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9-dependent innate immune responses in the liver. Blood 2011, 117:6459-6468. 10.1182/blood-2010-10-314518, 3123017, 21474674.
    • (2011) Blood , vol.117 , pp. 6459-6468
    • Martino, A.T.1    Suzuki, M.2    Markusic, D.M.3    Zolotukhin, I.4    Ryals, R.C.5    Moghimi, B.6    Ertl, H.C.7    Muruve, D.A.8    Lee, B.9    Herzog, R.W.10
  • 7
    • 44049090692 scopus 로고    scopus 로고
    • AAV-mediated gene transfer for the treatment of hemophilia B: problems and prospects
    • 10.1038/gt.2008.71, 18432276
    • Hasbrouck NC, High KA. AAV-mediated gene transfer for the treatment of hemophilia B: problems and prospects. Gene Ther 2008, 15:870-875. 10.1038/gt.2008.71, 18432276.
    • (2008) Gene Ther , vol.15 , pp. 870-875
    • Hasbrouck, N.C.1    High, K.A.2
  • 8
    • 57749190573 scopus 로고    scopus 로고
    • Genetic modification of adeno-associated viral vector type 2 capsid enhances gene transfer efficiency in polarized human airway epithelial cells
    • 10.1089/hum.2008.117, 18778196
    • White AF, Mazur M, Sorscher EJ, Zinn KR, Ponnazhagan S. Genetic modification of adeno-associated viral vector type 2 capsid enhances gene transfer efficiency in polarized human airway epithelial cells. Hum Gene Ther 2008, 19:1407-1414. 10.1089/hum.2008.117, 18778196.
    • (2008) Hum Gene Ther , vol.19 , pp. 1407-1414
    • White, A.F.1    Mazur, M.2    Sorscher, E.J.3    Zinn, K.R.4    Ponnazhagan, S.5
  • 10
    • 0031906147 scopus 로고    scopus 로고
    • Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions
    • 124624, 9445046
    • Summerford C, Samulski RJ. Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions. J Virol 1998, 72:1438-1445. 124624, 9445046.
    • (1998) J Virol , vol.72 , pp. 1438-1445
    • Summerford, C.1    Samulski, R.J.2
  • 11
    • 0038618725 scopus 로고    scopus 로고
    • Identification of amino acid residues in the capsid proteins of adeno-associated virus type 2 that contribute to heparan sulfate proteoglycan binding
    • 10.1128/JVI.77.12.6995-7006.2003, 156206, 12768018
    • Opie SR, Warrington KH, Agbandje-McKenna M, Zolotukhin S, Muzyczka N. Identification of amino acid residues in the capsid proteins of adeno-associated virus type 2 that contribute to heparan sulfate proteoglycan binding. J Virol 2003, 77:6995-7006. 10.1128/JVI.77.12.6995-7006.2003, 156206, 12768018.
    • (2003) J Virol , vol.77 , pp. 6995-7006
    • Opie, S.R.1    Warrington, K.H.2    Agbandje-McKenna, M.3    Zolotukhin, S.4    Muzyczka, N.5
  • 12
    • 0033851104 scopus 로고    scopus 로고
    • Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism
    • 10.1128/JVI.74.18.8635-8647.2000, 102071, 10954565
    • Wu P, Xiao W, Conlon T, Hughes J, Agbandje-McKenna M, Ferkol T, Flotte T, Muzyczka N. Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism. J Virol 2000, 74:8635-8647. 10.1128/JVI.74.18.8635-8647.2000, 102071, 10954565.
    • (2000) J Virol , vol.74 , pp. 8635-8647
    • Wu, P.1    Xiao, W.2    Conlon, T.3    Hughes, J.4    Agbandje-McKenna, M.5    Ferkol, T.6    Flotte, T.7    Muzyczka, N.8
  • 13
    • 69249213448 scopus 로고    scopus 로고
    • A muscle-targeting peptide displayed on AAV2 improves muscle tropism on systemic delivery
    • 10.1038/gt.2009.59, 2726895, 19474807
    • Yu CY, Yuan Z, Cao Z, Wang B, Qiao C, Li J, Xiao X. A muscle-targeting peptide displayed on AAV2 improves muscle tropism on systemic delivery. Gene Ther 2009, 16:953-962. 10.1038/gt.2009.59, 2726895, 19474807.
    • (2009) Gene Ther , vol.16 , pp. 953-962
    • Yu, C.Y.1    Yuan, Z.2    Cao, Z.3    Wang, B.4    Qiao, C.5    Li, J.6    Xiao, X.7
  • 15
    • 0034963928 scopus 로고    scopus 로고
    • Incorporation of tumor-targeting peptides into recombinant adeno-associated virus capsids
    • 10.1006/mthe.2001.0345, 11407911
    • Grifman M, Trepel M, Speece P, Gilbert LB, Arap W, Pasqualini R, Weitzman MD. Incorporation of tumor-targeting peptides into recombinant adeno-associated virus capsids. Mol Ther 2001, 3:964-975. 10.1006/mthe.2001.0345, 11407911.
    • (2001) Mol Ther , vol.3 , pp. 964-975
    • Grifman, M.1    Trepel, M.2    Speece, P.3    Gilbert, L.B.4    Arap, W.5    Pasqualini, R.6    Weitzman, M.D.7
  • 16
    • 0034056847 scopus 로고    scopus 로고
    • Selective drug delivery system to bone: small peptide (Asp)6 conjugation
    • Kasugai S, Fujisawa R, Waki Y, Miyamoto K, Ohya K. Selective drug delivery system to bone: small peptide (Asp)6 conjugation. J Bone Miner Res 2000, 15:936-943.
    • (2000) J Bone Miner Res , vol.15 , pp. 936-943
    • Kasugai, S.1    Fujisawa, R.2    Waki, Y.3    Miyamoto, K.4    Ohya, K.5
  • 17
    • 33745497185 scopus 로고    scopus 로고
    • Enhancement of drug delivery to bone: characterization of human tissue-nonspecific alkaline phosphatase tagged with an acidic oligopeptide
    • 10.1016/j.ymgme.2006.02.012, 2587042, 16616566
    • Nishioka T, Tomatsu S, Gutierrez MA, Miyamoto K, Trandafirescu GG, Lopez PL, Grubb JH, Kanai R, Kobayashi H, Yamaguchi S, et al. Enhancement of drug delivery to bone: characterization of human tissue-nonspecific alkaline phosphatase tagged with an acidic oligopeptide. Mol Genet Metab 2006, 88:244-255. 10.1016/j.ymgme.2006.02.012, 2587042, 16616566.
    • (2006) Mol Genet Metab , vol.88 , pp. 244-255
    • Nishioka, T.1    Tomatsu, S.2    Gutierrez, M.A.3    Miyamoto, K.4    Trandafirescu, G.G.5    Lopez, P.L.6    Grubb, J.H.7    Kanai, R.8    Kobayashi, H.9    Yamaguchi, S.10
  • 18
    • 77953140333 scopus 로고    scopus 로고
    • Enhancement of drug delivery: enzyme-replacement therapy for murine Morquio A syndrome
    • 10.1038/mt.2010.32, 2889747, 20332769
    • Tomatsu S, Montano AM, Dung VC, Ohashi A, Oikawa H, Oguma T, Orii T, Barrera L, Sly WS. Enhancement of drug delivery: enzyme-replacement therapy for murine Morquio A syndrome. Mol Ther 2010, 18:1094-1102. 10.1038/mt.2010.32, 2889747, 20332769.
    • (2010) Mol Ther , vol.18 , pp. 1094-1102
    • Tomatsu, S.1    Montano, A.M.2    Dung, V.C.3    Ohashi, A.4    Oikawa, H.5    Oguma, T.6    Orii, T.7    Barrera, L.8    Sly, W.S.9
  • 19
    • 81855216435 scopus 로고    scopus 로고
    • Rescue of severe infantile hypophosphatasia mice by AAV-mediated sustained expression of soluble alkaline phosphatase
    • 10.1089/hum.2010.210, 21388343
    • Matsumoto T, Miyake K, Yamamoto S, Orimo H, Miyake N, Odagaki Y, Adachi K, Iijima O, Narisawa S, Millan JL, et al. Rescue of severe infantile hypophosphatasia mice by AAV-mediated sustained expression of soluble alkaline phosphatase. Hum Gene Ther 2011, 22(11):1355-1364. 10.1089/hum.2010.210, 21388343.
    • (2011) Hum Gene Ther , vol.22 , Issue.11 , pp. 1355-1364
    • Matsumoto, T.1    Miyake, K.2    Yamamoto, S.3    Orimo, H.4    Miyake, N.5    Odagaki, Y.6    Adachi, K.7    Iijima, O.8    Narisawa, S.9    Millan, J.L.10
  • 22
    • 16844383364 scopus 로고    scopus 로고
    • Evaluation of the patient with muscle weakness
    • Saguil A. Evaluation of the patient with muscle weakness. Am Fam Physician 2005, 71:1327-1336.
    • (2005) Am Fam Physician , vol.71 , pp. 1327-1336
    • Saguil, A.1


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.