Failure of repeated cyclophosphamide pulse therapy in childhood cerebral X-linked adrenoleukodystrophy

Neuropediatrics

Volumn 43, Issue 1, 2012, Pages 48-52

  Horvath, Gabriellaana ^a   Eichler, Florian ^b   Poskitt, Ken ^a   Stockler Ipsiroglu, Sylvia ^a  

^a BC CHILDREN S HOSPITAL   (Canada)

^b MASSACHUSETTS GENERAL HOSPITAL   (United States)

Author keywords

adrenoleukodystrophy; cyclophosphamide; immunosuppression

Indexed keywords

ALBUMIN; CHOLINE; CREATINE; CYCLOPHOSPHAMIDE; GADOLINIUM; IMMUNOGLOBULIN G; MESNA; METHYLPREDNISOLONE; MEVINOLIN; N ACETYLASPARTIC ACID;

ABSENCE OF SIDE EFFECTS; ADRENOLEUKODYSTROPHY; ANGER; ARTICLE; CASE REPORT; CAUSE OF DEATH; CEREBROSPINAL FLUID ANALYSIS; CHILD; CHILDHOOD DISEASE; CLINICAL FEATURE; DEMYELINATION; DISEASE COURSE; DRUG DOSE INCREASE; DRUG PULSE THERAPY; DRUG TREATMENT FAILURE; EPILEPTIC STATE; GAIT DISORDER; HUMAN; IMMUNOGLOBULIN PRODUCTION; LEUKOCYTE COUNT; MAINTENANCE DRUG DOSE; MALE; NEUROIMAGING; NEUROLOGIC EXAMINATION; NUCLEAR MAGNETIC RESONANCE IMAGING; NUCLEAR MAGNETIC RESONANCE SPECTROSCOPY; PRESCHOOL CHILD; PRIORITY JOURNAL; PSYCHOSOCIAL WITHDRAWAL; REPEATED DRUG DOSE; RESPIRATORY FAILURE; SCHOOL CHILD; WHITE MATTER;

ADRENOLEUKODYSTROPHY; CHILD; CYCLOPHOSPHAMIDE; HUMANS; IMMUNOSUPPRESSIVE AGENTS; MAGNETIC RESONANCE IMAGING; MALE; TREATMENT FAILURE;

EID: 84858310871     PISSN: 0174304X     EISSN: 14391899     Source Type: Journal    
DOI: 10.1055/s-0032-1307455     Document Type: Article

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