Correction of murine bernard-soulier syndrome by lentivirus-mediated gene therapy

Molecular Therapy

Volumn 20, Issue 3, 2012, Pages 625-632

  Kanaji, Sachiko ^a   Kuether, Erin L ^a,b,c   Fahs, Scot A ^a   Schroeder, Jocelyn A ^a,b,c   Ware, Jerry ^d   Montgomery, Robert R ^a,b,c   Shi, Qizhen ^a,b,c  

^a BLOOD RESEARCH INSTITUTE   (United States)

^b MEDICAL COLLEGE OF WISCONSIN   (United States)

^c Children's Hospital and Health Systems   (United States)

^d UNIVERSITY OF ARKANSAS FOR MEDICAL SCIENCES   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

GLYCOPROTEIN IB ALPHA; GLYCOPROTEIN IIB IB ALPHA; LENTIVIRUS VECTOR; UNCLASSIFIED DRUG;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ANTIBODY RESPONSE; ARTICLE; BERNARD SOULIER DISEASE; BLEEDING TIME; BONE MARROW TRANSPLANTATION; CONTROLLED STUDY; DRUG EFFICACY; HEMATOPOIETIC STEM CELL; IMMUNE RESPONSE; IMMUNOPRECIPITATION; MOUSE; NONHUMAN; PHENOTYPE; PROMOTER REGION; PROTEIN EXPRESSION; PROTEIN LOCALIZATION; SIGNAL TRANSDUCTION; THROMBOCYTE COUNT; THROMBOCYTOPENIA; TRANSGENE; VIRAL GENE DELIVERY SYSTEM;

LENTIVIRUS; MURINAE; MUS;

EID: 84857781525     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2011.231     Document Type: Article

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