Bone marrow transplant options and preferences in a sickle cell anemia cohort on chronic transfusions

Pediatric Blood and Cancer

Volumn 58, Issue 4, 2012, Pages 611-615

  Hansbury, Eileen N ^a   Schultz, William H ^a   Ware, Russell E ^a   Aygun, Banu ^b  

^a BAYLOR COLLEGE OF MEDICINE   (United States)

^b ST JUDE CHILDREN S RESEARCH HOSPITAL   (United States)

Author keywords

Decision making; Sickle cell; Transplantation

Indexed keywords

ACUTE CHEST SYNDROME; ADOLESCENT; ARTICLE; BLOOD TRANSFUSION; BONE MARROW TRANSPLANTATION; CHILD; CONTROLLED STUDY; DATA ANALYSIS; DONOR; FAMILY; FEAR; FEMALE; HLA SYSTEM; HLA TYPING; HUMAN; MAJOR CLINICAL STUDY; MALE; PRESCHOOL CHILD; PRIORITY JOURNAL; QUALITY OF LIFE; RETROSPECTIVE STUDY; SCHOOL CHILD; SIBLING; SICKLE CELL ANEMIA; STROKE; TREATMENT INDICATION; TREATMENT REFUSAL;

ADOLESCENT; ANEMIA, SICKLE CELL; BLOOD TRANSFUSION; BONE MARROW TRANSPLANTATION; CHILD; CHILD, PRESCHOOL; FEMALE; HISTOCOMPATIBILITY TESTING; HUMANS; INFANT; MALE; RETROSPECTIVE STUDIES; TRANSPLANTATION, HOMOLOGOUS;

EID: 84856874131     PISSN: 15455009     EISSN: 15455017     Source Type: Journal    
DOI: 10.1002/pbc.23304     Document Type: Article

References (29)

1. Panepinto JA, Walters MC, Carreras J, et al. Matched-related donor transplantation for sickle cell disease: Report from the Center for International Blood and Transplant Research. Br J Haematol 2007; 137: 479-485.
2. Krishnamurti L, Bunn HF, Williams AM, et al. Hematopoietic cell transplantation for hemoglobinopathies. Curr Prob Pediatr Adol Health Care 2008; 38: 6-18.
3. Michlitsch JB, Walters MC. Recent advances in bone marrow transplantation in hemoglobinopathies. Curr Mol Med 2008; 8: 675-689.
4. Johnson FL, Look AT, Gockerman J, et al. Bone-marrow transplantation in a patient with sickle-cell anemia. N Engl J Med 1984; 311: 780-783.
5. Walters MC, Patience M, Leisenring W, et al. Bone marrow transplantation for sickle cell disease. N Engl J Med 1996; 335: 369-376.
6. Vermylen C, Cornu G, Ferster A, et al. Haematopoietic stem cell transplantation for sickle cell anaemia: The first 50 patients transplanted in Belgium. Bone Marrow Transplant 1998; 22: 1-6.
7. Bernaudin F, Socie G, Kuentz M, et al. Long-term results of related myeloablative stem-cell transplantation to cure sickle cell disease. Blood 2007; 110: 2749-2756.
8. Brousseau DC, Panepinto JA, Nimmer M, et al. The number of people with sickle-cell disease in the United States: National and state estimates. Am J Hematol 2010; 85: 77-78.
9. Weatherall DJ. The inherited diseases of hemoglobin are an emerging global health burden. Blood 2010; 115: 4331-4336.
10. Walters MC, Patience M, Leisenring W, et al. Barriers to bone marrow transplantation for sickle cell anemia. Biol Blood Marrow Transplant 1996; 2: 100-104.
11. Hsieh MM, Fitzhugh CD, Tisdale JF. Allogeneic hematopoietic stem cel transplant for sickle cell disease: The time is now. Blood 2011. [Epub ahead of print].
12. Kodish E, Lantos J, Stocking C, et al. Bone marrow transplantation for sickle cell disease: A study of parents' decisions. N Engl J Med 1991; 325: 1349-1353.
13. Kamani N, Lantos JD, Myers D, et al. Ethical considerations in pediatric BMT donors and recipients. Biol Blood Marrow Transplant 2011; 17: S132-S136.
14. Reed W, Smith R, Dekovic F, et al. Comprehensive banking of sibling donor cord blood for children with malignant and nonmalignant disease. Blood 2003; 101: 351-357.
15. Haywood C, Jr., Beach MC, Lanzkron S, et al. A systematic review of barriers and interventions to improve appropriate use of therapies for sickle cell disease. J Natl Med Assoc 2009; 101: 1022-1033.
16. Hankins J, Hinds P, Day S, et al. Therapy preference and decision-making among patients with severe sickle cell anemia and their families. Pediatr Blood Cancer 2007; 48: 705-710.
17. O'Brien SH, Hankins JS. Decision analysis of treatment strategies in children with severe sickle cell disease. J Pediatr Hematol Oncol 2009; 31: 873-878.
18. Panepinto JA, Pajewski NM, Foerster LM, et al. The performance of the PedsQL generic core scales in children with sickle cell disease. J Pediatr Hematol Oncol 2008; 30: 666-673.
19. Panepinto JA, Torres S, Varni JW. Development of the PedsQL sickle cell disease module items: Qualitative methods. Qual Life Res 2011. [Epub ahead of print].
20. American Academy of Pediatrics. Committee on Bioethics. Children as hematopoietic stem cell donors. Pediatrics 2010; 125: 392-404.
21. Revera GH, Frangoul H. A parent's point of view on the American Academy of Pediatrics policy statement: Children as hematopoietic stem cell donors. Pediatr Blood Cancer 2011; 56: 515-516.
22. Joffe S, Kodish E. Protecting the rights and interests of pediatric stem cell donors. Pediatr Blood Cancer 2011; 56: 517-519.
23. Anderson-Shaw L, Orfali K. Child-to-parent bone marrow donation for treatment of sickle cell disease. J Clin Ethics 2006; 17: 53-61.
24. Brodsky RA, Luznik L, Bolanos-Meade J, et al. Reduced intensity HLA-haploidentical BMT with post transplantation cyclophosphamide in nonmalignant hematologic diseases. Bone Marrow Transplant 2008; 42: 523-527.
25. Adamkiewicz TV, Szabolcs P, Haight A, et al. Unrelated cord blood transplantation in children with sickle cell disease: Review of four-center experience. Pediatr Transplant 2007; 11: 641-644.
26. Lukusa AK, Vermylen C, Vanabelle B, et al. Bone marrow transplantation or hydroxyurea for sickle cell anemia: Long-term effects on semen variables and hormone profiles. Pediatr Hematol Oncol 2009; 26: 186-194.
27. Walters MC, Hardy K, Edwards S, et al. Pulmonary, gonadal, and central nervous system status after bone marrow transplantation for sickle cell disease. Biol Blood Marrow Transplant 2010; 16: 263-272.
28. Roux C, Amiot C, Agnani G, et al. Live birth after ovarian tissue autograft in a patient with sickle cell disease treated by allogeneic bone marrow transplantation. Fertil Steril 2010; 93: 2413.
29. Hulbert ML, McKinstry RC, Lacey JL, et al. Silent cerebral infarcts occur despite regular blood transfusion therapy after first strokes in children with sickle cell disease. Blood 2011; 117: 772-779.