Genistein in Sanfilippo disease: A randomized controlled crossover trial

Annals of Neurology

Volumn 71, Issue 1, 2012, Pages 110-120

  De Ruijter, Jessica ^a   Valstar, Marlies J ^a   Narajczyk, Magdalena ^b   Wegrzyn, Grzegorz ^b   Kulik, Wim ^a   Ijlst, Lodewijk ^a   Wagemans, Tom ^a   Van Der Wal, Willem M ^c   Wijburg, Frits A ^a  

^a UNIVERSITY OF AMSTERDAM   (Netherlands)

^b UNIVERSITY OF GDA SK   (Poland)

^c UNIVERSITY MEDICAL CENTER UTRECHT   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

GENISTEIN; GLYCOSAMINOGLYCAN; HEPARAN SULFATE;

ADOLESCENT; ADULT; AGED; ARTICLE; BEHAVIOR; BLOOD SAMPLING; CHILD; CLINICAL ARTICLE; CONTROLLED STUDY; CROSSOVER PROCEDURE; DOUBLE BLIND PROCEDURE; DRUG BLOOD LEVEL; DRUG EFFICACY; FEMALE; GLYCOSAMINOGLYCAN METABOLISM; HAIR ANALYSIS; HUMAN; MALE; OPEN STUDY; OUTCOME ASSESSMENT; PHYSICAL EXAMINATION; PRESCHOOL CHILD; PRIORITY JOURNAL; RANDOMIZED CONTROLLED TRIAL; SANFILIPPO SYNDROME; SCHOOL CHILD; TABLET; TREATMENT DURATION; URINALYSIS; URINARY EXCRETION;

ADOLESCENT; ADULT; AGED; CHILD; CHILD, PRESCHOOL; CROSS-OVER STUDIES; DOUBLE-BLIND METHOD; FEMALE; GENISTEIN; GLYCOSAMINOGLYCANS; HUMANS; LONGITUDINAL STUDIES; MALE; MIDDLE AGED; MUCOPOLYSACCHARIDOSIS III; YOUNG ADULT;

EID: 84856199028     PISSN: 03645134     EISSN: 15318249     Source Type: Journal    
DOI: 10.1002/ana.22643     Document Type: Article

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