Advances in allogeneic stem cell transplantation for hemoglobinopathies

Hemoglobin

Volumn 35, Issue 5-6, 2011, Pages 469-475

  Al Jefri, Abdullah H ^a  

^a KING FAISAL SPECIALIST HOSPITAL AND RESEARCH CENTER   (Saudi Arabia)

Author keywords

Allogeneic stem cell transplantation (SCT); Hemoglobinopathies; Sickle cell anemia; Thalassemia

Indexed keywords

AZATHIOPRINE; BUSULFAN; CYCLOPHOSPHAMIDE; CYCLOSPORIN A; DEFEROXAMINE; FLUDARABINE; GRANULOCYTE COLONY STIMULATING FACTOR; HEMOGLOBIN; HYDROXYUREA; RECOMBINANT ERYTHROPOIETIN; STEROID; THIOTEPA; THYMOCYTE ANTIBODY;

ACUTE CHEST SYNDROME; ALLOGENEIC STEM CELL TRANSPLANTATION; ALLOIMMUNIZATION; ARTICLE; BETA THALASSEMIA; BLOOD TRANSFUSION; BONE NECROSIS; CELL SURVIVAL; CHILDHOOD DISEASE; CHIMERA; CLINICAL PROTOCOL; CORD BLOOD STEM CELL TRANSPLANTATION; DISEASE CLASSIFICATION; DISEASE FREE SURVIVAL; DISEASE SEVERITY; DRUG DOSE SEQUENCE; EVENT FREE SURVIVAL; FRANCE; GRAFT REJECTION; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL; HEMOGLOBIN BLOOD LEVEL; HEMOGLOBINOPATHY; HEPATOMEGALY; HUMAN; IMMUNOSUPPRESSIVE TREATMENT; IRON CHELATION; LIVER FIBROSIS; LIVING DONOR; MEDICAL HISTORY; MORTALITY; MULTICENTER STUDY (TOPIC); MYELOABLATIVE CONDITIONING; NONMYELOABLATIVE CONDITIONING; RECURRENT DISEASE; REDUCED INTENSITY CONDITIONING; REPEAT PROCEDURE; SAUDI ARABIA; SICKLE CELL ANEMIA; STEROID THERAPY; STROKE; TISSUE TYPING; TREATMENT INDICATION; TREATMENT OUTCOME;

ANEMIA, SICKLE CELL; BETA-THALASSEMIA; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOGLOBINOPATHIES; HUMANS; RECURRENCE; TRANSPLANTATION CONDITIONING; TRANSPLANTATION, HOMOLOGOUS;

EID: 81055125416     PISSN: 03630269     EISSN: 1532432X     Source Type: Journal    
DOI: 10.3109/03630269.2011.618567     Document Type: Article

References (24)

1. Locatelli, F, Stefano, PD. New insights into haematopoietic stem cell transplantation for patients with haemoglobinopathies. Br J Haematol. 2004;125(1):3-11. (Pubitemid 38453271)
2. Lucarelli, G, Polchi, P, Izzi, T, et al. Allogeneic marrow transplantation for thalassemia. Exp Hematol. 1984;12(8):676-681. (Pubitemid 14006602)
3. Lucarelli, G, Galimberti, M, Polchi, P, et al. Bone marrow transplantation in patients with thalassemia. N Engl J Med. 1990;322(7):417-421. (Pubitemid 20059509)
4. Lucarelli, G, Galimberti, M, Polchi, P, et al. Bone marrow transplantation in thalassemia. Hematol Oncol Clin North Am. 1991;5(3):549-556.
5. Lucarelli, G, Clift, RA, Galimberti, M, et al. Marrow transplantation for patients with thalassemia. Results in class 3 patients. Blood. 1996;87(5):2082-2088. (Pubitemid 26068926)
6. Lucarelli, G, Clift, RA, Galimberti, M, et al. Bone marrow transplantation in adult thalassemic patients. Blood. 1999;93(4):1164-1167. (Pubitemid 29076130)
7. Gaziev J, Sodani P, Polchi P, Andreani M, Lucarelli G. Bone marrow transplantation in adults with thalassemia: treatment and long-term follow-up. Ann NY Acad Sci. 2005;1054:196-205. (Pubitemid 43031025)
8. Sodani P, Gaziev D, Polchi P, et al. New approach for bone marrow transplantation in patients with class 3 thalassemia aged younger than 17 years. Blood. 2004;104(4):1201-1203. (Pubitemid 39038044)
9. Gaziev J, Sodani P, Lucarelli G, et al. Second hematopoietic SCT in patients with thalassemia recurrence following rejection of the first graft. Bone Marrow Transplant. 2008;42(6):397-404.
10. La Nasa G, Caocci G, Argiolu F, et al. Unrelated donor stem cell transplantation in adult patients with thalassemia. Bone Marrow Transplant. 2005;36(11):971-975. (Pubitemid 41741560)
11. La Nasa G, Argiolu F, Giardini C, et al. Unrelated bone marrow transplantation for β-thalassemia patients: The experience of the Italian Bone Marrow Transplant Group. Ann NY Acad Sci. 2005;1054:186-195. (Pubitemid 43031024)
12. Locatelli F, Rocha V, Reed W, et al. Related umbilical cord blood transplantation in patients with thalassemia and sickle cell disease. Blood. 2003;101(6):2137-2143. (Pubitemid 36302049)
13. Locatelli F, De Stephano P. Innovative approaches to hematopoietic stem cell transplantation for patients with thalassemia. Haematologica. 2005;90(12):1592-1594. (Pubitemid 41818989)
14. Iannone R, Casella JF, Fuch EJ, Chen AR, Jones RJ, Woolfrey A. Results of minimally toxic nonmyeloablative transplantation in patients with sickle cell anemia and β-thalassemia. Biol Blood Marrow Transplant. 2003;9(8):519-528. (Pubitemid 38351796)
15. Iannone R, Ohene-Frempong K, Fuchs EJ, Casella JF, Chen AR. Bone marrow transplantation for sickle cell anemia: progress and prospects. Pediatr Blood Cancer. 2005;44(5):436-440. (Pubitemid 40614490)
16. Walters MC, Storb R, Patience M, et al. Impact of bone marrow transplantation for symptomatic sickle cell disease: interim report. Multicenter investigation of bone marrow transplantation for sickle cell disease. Blood. 2000;95(6):1918-1194.
17. Walters MC, Patience M, Leisenring W, et al. Bone marrow transplantation for sickle cell disease. N Engl J Med. 1996;335(6):369-376. (Pubitemid 26257244)
18. Vermylen C, Cornu G, Ferster A, et al. Haematopoietic stem cell transplantation for sickle cell anaemia: the first 50 patients transplanted in Belgium. Bone Marrow Transplant. 1998;22(1):1-6. (Pubitemid 28330528)
19. Buchanan GR, DeBaun MR, Quinn CT, Steinberg MH. Sickle cell disease. Hematology Am Soc Hematol Educ Program. 2004;35-47.
20. Hoppe CC, Walters MC. Bone marrow transplantation in sickle cell anemia. Curr Opin Oncol. 2001;13(2):85-90. (Pubitemid 32242854)
21. Bernaudin F, Socie G, Kuentz M, et al. Long-term results of related myeloablative stem-cell transplantation to cure sickle cell disease. Blood. 2007;110(7):2749-2756. (Pubitemid 47523201)
22. Horan JT, Liesveld JL, Fenton P, Blumberg N, Walters MC. Hematopoietic stem cell transplantation for multiply transfused patients with sickle cell disease and thalassemia after low-dose total body irradiation, fludarabine and rabbit anti-thymocyte globulin. Bone Marrow Transplant. 2005;35(2):171-177. (Pubitemid 40185933)
23. Hsieh M, Kang E, Fitzhugh C, et al. Allogeneic hematopoietic stem cell transplantation in sickle cell disease. N Engl J Med. 2009;361(24):2309-2317.
24. Al Jefri A, Ayas M, Al Musa M, et al. Allogeneic stem cell transplantation in patients with β-thalassemia: King Faisal Specialist Hospital and Research Center experience. Hemoglobin.2009;33(S1):S183-S187.