Helper-dependent canine adenovirus vector-mediated transgene expression in a neurodegenerative lysosomal storage disorder

Gene

Volumn 491, Issue 1, 2012, Pages 53-57

  Lau, Adeline A ^a   Rozaklis, Tina ^a   Ibanes, Sandy ^c,d   Luck, Amanda J ^a   Beard, Helen ^a   Hassiotis, Sofia ^a   Mazouni, Khalil ^c,d,e   Hopwood, John J ^a,b   Kremer, Eric J ^c,d   Hemsley, Kim M ^a,b  

^a WOMEN S AND CHILDREN S HOSPITAL   (Australia)

^b UNIVERSITY OF ADELAIDE   (Australia)

^c INSTITUT DE GÉNÉTIQUE MOLÉCULAIRE DE MONTPELLIER   (France)

^d UNIV MONTPELLIER   (France)

^e INSTITUT PASTEUR   (France)

Author keywords

Canine adenovirus; Gene therapy; Lysosomal storage disease; Mucopolysaccharidosis; Sanfilippo syndrome

Indexed keywords

ADENOVIRUS VECTOR; HEPARAN SULFATE;

ANIMAL TISSUE; ARTICLE; CANINE ADENOVIRUS; CELL CULTURE; CONTROLLED STUDY; DEGENERATIVE DISEASE; GENE EXPRESSION; GENE THERAPY; GENE VECTOR; MOUSE; MUCOPOLYSACCHARIDOSIS; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; STORAGE DISEASE;

ADENOVIRUSES, CANINE; ANIMALS; BRAIN; CELLS, CULTURED; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HELPER VIRUSES; HYDROLASES; MUCOPOLYSACCHARIDOSIS III; TRANSGENES;

CANINE ADENOVIRUS; MUS;

EID: 80055077105     PISSN: 03781119     EISSN: 18790038     Source Type: Journal    
DOI: 10.1016/j.gene.2011.09.004     Document Type: Article

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