-
1
-
-
78650858386
-
The complex and evolving story of T cell activation to AAV vector-encoded transgene products
-
Mays LE, Wilson JM. The complex and evolving story of T cell activation to AAV vector-encoded transgene products. Mol. Ther. 19(1), 16-27 (2011).
-
(2011)
Mol. Ther.
, vol.19
, Issue.1
, pp. 16-27
-
-
Mays, L.E.1
Wilson, J.M.2
-
3
-
-
27544495302
-
Chromatographic purification of recombinant adenoviral and adeno-associated viral vectors: Methods and implications
-
DOI 10.1038/sj.gt.3302611, PII 3302611
-
Burova E, Ioffe E. Chromatographic purifcation of recombinant adenoviral and adeno-associated viral vectors: methods and implications. Gene Ther. 12(Suppl. 1), S5-S17 (2005). (Pubitemid 41541749)
-
(2005)
Gene Therapy
, vol.12
, Issue.SUPPL. 1
-
-
Burova, E.1
Ioffe, E.2
-
4
-
-
80054062407
-
Peptide affnity reagents for AAV capsid recognition and purifcation
-
DOI:10.1038/gt.2011.46 Epub ahead of print
-
Pulicherla N, Asokan A. Peptide affnity reagents for AAV capsid recognition and purifcation. Gene Ther. DOI:10.1038/gt.2011.46 (2011) (Epub ahead of print).
-
(2011)
Gene Ther.
-
-
Pulicherla, N.1
Asokan, A.2
-
5
-
-
79954622209
-
Therapeutic in vivo gene transfer for genetic disease using AAV: Progress and challenges
-
Mingozzi F, High KA. Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges. Nat. Rev. Genet. 12(5), 341-355 (2011).
-
(2011)
Nat. Rev. Genet.
, vol.12
, Issue.5
, pp. 341-355
-
-
Mingozzi, F.1
High, K.A.2
-
6
-
-
48949120141
-
Recent developments in adeno-associated virus vector technology
-
DOI 10.1002/jgm.1205
-
Buning H, Perabo L, Coutelle O, Quadt-Humme S, Hallek M. Recent developments in adeno-associated virus vector technology. J. Gene Med. 10(7), 717-733 (2008). (Pubitemid 352003915)
-
(2008)
Journal of Gene Medicine
, vol.10
, Issue.7
, pp. 717-733
-
-
Buning, H.1
Perabo, L.2
Coutelle, O.3
Quadt-Humme, S.4
Hallek, M.5
-
7
-
-
79952169637
-
Diversity of phage-displayed libraries of peptides during panning and amplifcation
-
Derda R, Tang SK, Li SC et al. Diversity of phage-displayed libraries of peptides during panning and amplifcation. Molecules 16(2), 1776-1803 (2011).
-
(2011)
Molecules
, vol.16
, Issue.2
, pp. 1776-1803
-
-
Derda, R.1
Tang, S.K.2
Li, S.C.3
-
8
-
-
65249116937
-
Successful expansion but not complete restriction of tropism of adeno-associated virus by in vivo biopanning of random virus display peptide libraries
-
Michelfelder S, Kohlschutter J, Skorupa A et al. Successful expansion but not complete restriction of tropism of adeno-associated virus by in vivo biopanning of random virus display peptide libraries. PLoS One 4(4), e5122 (2009).
-
(2009)
PLoS One
, vol.4
, Issue.4
-
-
Michelfelder, S.1
Kohlschutter, J.2
Skorupa, A.3
-
9
-
-
77955654722
-
Heart-targeted adeno-associated viral vectors selected by in vivo biopanning of a random viral display peptide library
-
Ying Y, Muller OJ, Goehringer C et al. Heart-targeted adeno-associated viral vectors selected by in vivo biopanning of a random viral display peptide library. Gene Ther. 17(8), 980-990 (2010).
-
(2010)
Gene Ther.
, vol.17
, Issue.8
, pp. 980-990
-
-
Ying, Y.1
Muller, O.J.2
Goehringer, C.3
-
10
-
-
44949131860
-
In vitro and in vivo gene therapy vector evolution via multispecies interbreeding and retargeting of adeno-associated viruses
-
DOI 10.1128/JVI.00254-08
-
Grimm D, Lee JS, Wang L et al. In vitro and in vivo gene therapy vector evolution via multispecies interbreeding and retargeting of adeno-associated viruses. J. Virol. 82 (12), 5887-5911 (2008). (Pubitemid 351822263)
-
(2008)
Journal of Virology
, vol.82
, Issue.12
, pp. 5887-5911
-
-
Grimm, D.1
Lee, J.S.2
Wang, L.3
Desai, T.4
Akache, B.5
Storm, T.A.6
Kay, M.A.7
-
11
-
-
73849091644
-
Molecular evolution of adeno-associated virus for enhanced glial gene delivery
-
Koerber JT, Klimczak R, Jang JH et al. Molecular evolution of adeno-associated virus for enhanced glial gene delivery. Mol. Ther. 17 (12), 2088-2095 (2009).
-
(2009)
Mol. Ther.
, vol.17
, Issue.12
, pp. 2088-2095
-
-
Koerber, J.T.1
Klimczak, R.2
Jang, J.H.3
-
12
-
-
77649273563
-
Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB)
-
Gray SJ, Blake BL, Criswell HE et al. Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB). Mol. Ther. 18(3), 570-578 (2010).
-
(2010)
Mol. Ther.
, vol.18
, Issue.3
, pp. 570-578
-
-
Gray, S.J.1
Blake, B.L.2
Criswell, H.E.3
-
13
-
-
73849130017
-
Generation of novel A AV variants by directed evolution for improved CFTR delivery to human ciliated airway epithelium
-
Li W, Zhang L, Johnson JS et al. Generation of novel A AV variants by directed evolution for improved CFTR delivery to human ciliated airway epithelium. Mol. Ther. 17(12), 2067-2077 (2009).
-
(2009)
Mol. Ther.
, vol.17
, Issue.12
, pp. 2067-2077
-
-
Li, W.1
Zhang, L.2
Johnson, J.S.3
-
14
-
-
45549090635
-
Next generation of adeno-associated virus 2 vectors: Point mutations in tyrosines lead to high-efficiency transduction at lower doses
-
DOI 10.1073/pnas.0802866105
-
Zhong L, Li B, Mah CS et al. Next generation of adeno-associated virus 2 vectors: point mutations in tyrosines lead to high-effciency transduction at lower doses. Proc. Natl Acad. Sci. USA 105(22), 7827-7832 (2008). (Pubitemid 351872723)
-
(2008)
Proceedings of the National Academy of Sciences of the United States of America
, vol.105
, Issue.22
, pp. 7827-7832
-
-
Zhong, L.1
Li, B.2
Mah, C.S.3
Govindasamy, L.4
Agbandje-McKenna, M.5
Cooper, M.6
Herzog, R.W.7
Zolotukhin, I.8
Warrington Jr., K.H.9
Weigel-Van Aken, K.A.10
Hobbs, J.A.11
Zolotukhin, S.12
Muzyczka, N.13
Srivastava, A.14
-
15
-
-
0141454787
-
Identification of a heparin-binding motif on adeno-associated virus type 2 capsids
-
DOI 10.1128/JVI.77.20.11072-11081.2003
-
Kern A, Schmidt K, Leder C et al. Identifcation of a heparin-binding motif on adeno-associated virus type 2 capsids. J. Virol. 77(20), 11072-11081 (2003). (Pubitemid 37204297)
-
(2003)
Journal of Virology
, vol.77
, Issue.20
, pp. 11072-11081
-
-
Kern, A.1
Schmidt, K.2
Leder, C.3
Muller, O.J.4
Wobus, C.E.5
Bettinger, K.6
Von Der Lieth, C.W.7
King, J.A.8
Kleinschmidt, J.A.9
-
16
-
-
0038618725
-
Identification of amino acid residues in the capsid proteins of adeno-associated virus type 2 that contribute to heparan sulfate proteoglycan binding
-
DOI 10.1128/JVI.77.12.6995-7006.2003
-
Opie SR, Warrington KH Jr, Agbandje-McKenna M, Zolotukhin S, Muzyczka N. Identifcation of amino acid residues in the capsid proteins of adeno-associated virus type 2 that contribute to heparan sulfate proteoglycan binding. J. Virol. 77(12), 6995-7006 (2003). (Pubitemid 36666892)
-
(2003)
Journal of Virology
, vol.77
, Issue.12
, pp. 6995-7006
-
-
Opie, S.R.1
Warrington Jr., K.H.2
Agbandje-McKenna, M.3
Zolotukhin, S.4
Muzyczka, N.5
-
17
-
-
33748494015
-
Adeno-associated virus type 2 contains an integrin α5β1 binding domain essential for viral cell entry
-
DOI 10.1128/JVI.00843-06
-
Asokan A, Hamra JB, Govindasamy L, Agbandje-McKenna M, Samulski RJ. Adeno-associated virus type 2 contains an integrin a5b1 binding domain essential for viral cell entry. J. Virol. 80(18), 8961-8969 (2006). (Pubitemid 44359970)
-
(2006)
Journal of Virology
, vol.80
, Issue.18
, pp. 8961-8969
-
-
Asokan, A.1
Hamra, J.B.2
Govindasamy, L.3
Agbandje-McKenna, M.4
Samulski, R.J.5
-
18
-
-
38349104204
-
Human CMV immediate-early enhancer: A useful tool to enhance cell-type-specifc expression from lentiviral vectors
-
Gruh I, Wunderlich S, Winkler M et al. Human CMV immediate-early enhancer: a useful tool to enhance cell-type-specifc expression from lentiviral vectors. J. Gene Med. 10 (1), 21-32 (2008).
-
(2008)
J. Gene Med.
, vol.10
, Issue.1
, pp. 21-32
-
-
Gruh, I.1
Wunderlich, S.2
Winkler, M.3
-
19
-
-
79954580272
-
Current prospects for RNA interference-based therapies
-
Davidson BL, McCray PB Jr. Current prospects for RNA interference-based therapies. Nat. Rev. Genet. 12(5), 329-40 (2011).
-
(2011)
Nat. Rev. Genet.
, vol.12
, Issue.5
, pp. 329-340
-
-
Davidson, B.L.1
McCray Jr., P.B.2
-
20
-
-
79951510234
-
MicroRNA122-regulated transgene expression increases specifcity of cardiac gene transfer upon intravenous delivery of AAV9 vectors
-
Geisler A, Jungmann A, Kurreck J et al. microRNA122-regulated transgene expression increases specifcity of cardiac gene transfer upon intravenous delivery of AAV9 vectors. Gene Ther. 18(2), 199-209 (2011).
-
(2011)
Gene Ther.
, vol.18
, Issue.2
, pp. 199-209
-
-
Geisler, A.1
Jungmann, A.2
Kurreck, J.3
-
21
-
-
79953803239
-
Liver-specifc microRNA-122 target sequences incorporated in A AV vectors effciently inhibits transgene expression in the liver
-
Qiao C, Yuan Z, Li J et al. Liver-specifc microRNA-122 target sequences incorporated in A AV vectors effciently inhibits transgene expression in the liver. Gene Ther. 18(4), 403-410 (2011).
-
(2011)
Gene Ther.
, vol.18
, Issue.4
, pp. 403-410
-
-
Qiao, C.1
Yuan, Z.2
Li, J.3
-
22
-
-
73949097812
-
Optimization of stealth adeno-associated virus vectors by randomization of immunogenic epitopes
-
Maersch S, Huber A, Buning H, Hallek M, Perabo L. Optimization of stealth adeno-associated virus vectors by randomization of immunogenic epitopes. Virology 397(1), 167-175 (2010).
-
(2010)
Virology
, vol.397
, Issue.1
, pp. 167-175
-
-
Maersch, S.1
Huber, A.2
Buning, H.3
Hallek, M.4
Perabo, L.5
-
23
-
-
79953793932
-
Capsid-expressing DNA in AAV vectors and its elimination by use of an oversize capsid gene for vector production
-
Halbert CL, Metzger MJ, Lam SL, Miller AD. Capsid-expressing DNA in AAV vectors and its elimination by use of an oversize capsid gene for vector production. Gene Ther. 18(4), 411-417 (2011).
-
(2011)
Gene Ther.
, vol.18
, Issue.4
, pp. 411-417
-
-
Halbert, C.L.1
Metzger, M.J.2
Lam, S.L.3
Miller, A.D.4
-
24
-
-
79955453097
-
Systemic elimination of de novo capsid protein synthesis from replication-competent A AV contamination in the liver
-
Lu H, Qu G, Yang X, Xu R, Xiao W. Systemic elimination of de novo capsid protein synthesis from replication-competent A AV contamination in the liver. Hum. Gene Ther. 22(5), 625-632 (2011).
-
(2011)
Hum. Gene Ther.
, vol.22
, Issue.5
, pp. 625-632
-
-
Lu, H.1
Qu, G.2
Yang, X.3
Xu, R.4
Xiao, W.5
|