X-ALD: Centralize care in an international network

Blood

Volumn 118, Issue 7, 2011, Pages 1716-1717

  Boelens, Jaap J ^a  

^a UNIVERSITY MEDICAL CENTER UTRECHT   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

ACETYLCYSTEINE;

ADJUVANT THERAPY; ADRENOLEUKODYSTROPHY; CELL THERAPY; CENTRALIZED CARE; CLINICAL PROTOCOL; CLINICAL RESEARCH; DISEASE COURSE; DISEASE SEVERITY; EARLY DIAGNOSIS; FOLLOW UP; GENE THERAPY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HURLER SYNDROME; METABOLIC DISORDER; MORBIDITY; NONMYELOABLATIVE CONDITIONING; NOTE; OVERALL SURVIVAL; PATIENT CARE; PATIENT SELECTION; PRACTICE GUIDELINE; PRIORITY JOURNAL; RARE DISEASE; SCORING SYSTEM; SURVIVAL RATE; TREATMENT OUTCOME; X CHROMOSOME LINKED DISORDER;

EID: 80051876592     PISSN: 00064971     EISSN: 15280020     Source Type: Journal    
DOI: 10.1182/blood-2011-06-356584     Document Type: Note

References (7)

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