Ceiling culture-derived proliferative adipocytes are a possible delivery vehicle for enzyme replacement therapy in Lecithin: Cholesterol acyltransferase deficiency

Open Gene Therapy Journal

Volumn 4, Issue 1, 2011, Pages 1-10

  Kuroda, Masayuki ^a,b,c   Aoyagi, Yasuyuki ^a,b,c   Asada, Sakiyo ^a,b,c   Bujo, Hideaki ^b   Tanaka, Shigeaki ^c   Konno, Shunichi ^c   Tanio, Masami ^c   Ishii, Itsuko ^b   Machida, Kazuhiko ^d   Matsumoto, Fumiaki ^b   Satoh, Kaneshige ^b   Aso, Masayuki ^c   Saito, Yasushi ^b  

^a CHIBA UNIVERSITY HOSPITAL   (Japan)

^b CHIBA UNIVERSITY   (Japan)

^c CellGenTech Inc   (Japan)

^d CENTRAL INSTITUTE FOR EXPERIMENTAL ANIMALS   (Japan)

Author keywords

Adipocyte; Ceiling culture; Gene therapy; Lecithin:cholesterol acyltransferase; Protein replacement therapy

Indexed keywords

PHOSPHATIDYLCHOLINE STEROL ACYLTRANSFERASE; RETROVIRUS VECTOR;

ADIPOCYTE; ADULT; ANIMAL EXPERIMENT; ARTICLE; CEILING CULTURE TECHNIQUE; CELL BASED GENE THERAPY; CELL DIFFERENTIATION; CELL TRANSPLANTATION; CONTROLLED STUDY; CULTURE TECHNIQUE; ENZYME ACTIVITY; ENZYME REPLACEMENT; GENE; GENE DOSAGE; HUMAN; HUMAN CELL; HUMAN TISSUE; IN VITRO STUDY; LCAT GENE; LECITHIN CHOLESTEROL ACYLTRANSFERASE DEFICIENCY; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROTEIN ANALYSIS; PROTEIN BLOOD LEVEL; SUBCUTANEOUS FAT; VIRAL GENE DELIVERY SYSTEM; VIRUS GENOME;

MUS;

EID: 79953274795     PISSN: None     EISSN: 18750370     Source Type: Journal    
DOI: 10.2174/1875037001104010001     Document Type: Article

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