The case for a global rare-diseases registry

The Lancet

Volumn 377, Issue 9771, 2011, Pages 1057-1059

  Forrest, Christopher B ^a,b   Bartek, Ronald J ^c   Rubinstein, Yaffa ^d   Groft, Stephen C ^d  

^a CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^b UNIVERSITY OF PENNSYLVANIA   (United States)

^c Friedreich's Ataxia Research Alliance (FARA)   (United States)

^d NATIONAL INSTITUTES OF HEALTH   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ORPHAN DRUG;

COST BENEFIT ANALYSIS; DISEASE REGISTRY; ELECTRONIC MEDICAL RECORD; HEALTH CARE SYSTEM; HUMAN; LIFESTYLE; MEDICAL RESEARCH; NOTE; PRIORITY JOURNAL; RARE DISEASE; UNITED STATES; WELLBEING;

EID: 79953161288     PISSN: 01406736     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0140-6736(10)60680-0     Document Type: Note

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