Long-term correction of murine phenylketonuria by viral gene transfer: Liver versus muscle

Journal of Inherited Metabolic Disease

Volumn 33, Issue 6, 2010, Pages 677-680

  Thöny, Beat ^a  

^a UNIVERSITY OF ZURICH   (Switzerland)

Author keywords

[No Author keywords available]

Indexed keywords

PHENYLALANINE; PHENYLALANINE 4 MONOOXYGENASE; TETRAHYDROBIOPTERIN; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ALTERNATIVE MEDICINE; AMINO ACID BLOOD LEVEL; DIET RESTRICTION; DNA SEQUENCE; DOSE RESPONSE; DRUG SYNTHESIS; EXPRESSION VECTOR; HUMAN; LONG TERM CARE; NONHUMAN; PHENOTYPE; PHENYLKETONURIA; PROTEIN EXPRESSION; REVIEW; SINGLE DRUG DOSE; SKELETAL MUSCLE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; ANIMAL; ANTIBODY SPECIFICITY; DISEASE MODEL; EVALUATION; GENE THERAPY; GENE TRANSFER; GENE VECTOR; GENETICS; LIVER; METABOLISM; METHODOLOGY; MOUSE; MUSCLE; PATHOLOGY; REMISSION; TIME;

ANIMALS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; LIVER; MICE; MUSCLES; ORGAN SPECIFICITY; PHENYLKETONURIAS; REMISSION INDUCTION; TIME FACTORS;

EID: 79952563525     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-010-9044-3     Document Type: Review

References (9)

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