Metabolic engineering as therapy for inborn errors of metabolism - Development of mice with phenylalanine hydroxylase expression in muscle

Gene Therapy

Volumn 5, Issue 5, 1998, Pages 677-683

  Harding, C O ^a   Wild, K ^a   Chang, D ^a   Messing, A ^a,b   Wolff, J A ^a  

^a UNIVERSITY OF WISCONSIN MADISON   (United States)

^b UNIVERSITY OF WISCONSIN SCHOOL OF MEDICINE AND PUBLIC HEALTH   (United States)

Author keywords

Inborn errors of metabolism; Muscle; Phenylketonuria

Indexed keywords

COMPLEMENTARY DNA; CREATINE KINASE; LIVER ENZYME; PHENYLALANINE; PHENYLALANINE 4 MONOOXYGENASE; TETRAHYDROBIOPTERIN;

AMINO ACID BLOOD LEVEL; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; ENZYME ACTIVITY; ENZYME DEFICIENCY; FEMALE; GENE THERAPY; HEART MUSCLE; HYPERPHENYLALANINEMIA; INBORN ERROR OF METABOLISM; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; SKELETAL MUSCLE; TRANSGENIC MOUSE;

ANIMALIA; MUS MUSCULUS;

EID: 0031834511     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300653     Document Type: Article

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