Tetrahydrobiopterin therapy for phenylketonuria in infants and young children

Journal of Pediatrics

Volumn 158, Issue 3, 2011, Pages 410-415

  Burton, Barbara K ^a   Adams, Darius J ^b   Grange, Dorothy K ^c   Malone, John I ^d   Jurecki, Elaina ^e   Bausell, Heather ^f   Marra, Kayt D ^b   Sprietsma, Laurie ^c   Swan, Kathleen T ^g  

^a NORTHWESTERN UNIVERSITY   (United States)

^b ALBANY MEDICAL CENTER   (United States)

^c WASHINGTON UNIVERSITY SCHOOL OF MEDICINE   (United States)

^d UNIVERSITY OF SOUTH FLORIDA   (United States)

^e BIOMARIN PHARMACEUTICAL INC   (United States)

^f CHILDREN'S MEMORIAL HOSPITAL   (United States)

^g UNIVERSITY OF SOUTH FLORIDA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

PHENYLALANINE; SAPROPTERIN;

ARTICLE; CASE REPORT; CHILD; CLINICAL ARTICLE; DIARRHEA; DIET; DISEASE SEVERITY; DRUG DOSE INCREASE; DRUG SAFETY; DRUG TOLERABILITY; GROUPS BY AGE; HUMAN; INFANT; OUTCOME ASSESSMENT; PATIENT MONITORING; PATIENT SELECTION; PHENYLKETONURIA; PRESCHOOL CHILD; PRIORITY JOURNAL; TREATMENT RESPONSE;

BIOPTERIN; CHILD, PRESCHOOL; FEMALE; HUMANS; INFANT; MALE; PATIENT SELECTION; PHENYLALANINE; PHENYLKETONURIAS; TREATMENT OUTCOME;

EID: 79951576257     PISSN: 00223476     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.jpeds.2010.08.016     Document Type: Article

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