Gene therapy by allele selection in a mouse model of beta-thalassemia

Journal of Clinical Investigation

Volumn 121, Issue 2, 2011, Pages 623-627

  Eckardt, Sigrid ^a   Leu, N Adrian ^b   Yanchik, Ashley ^b   Hatada, Seigo ^c,f   Kyba, Michael ^d   McLaughlin, K John ^a,e  

^a THE RESEARCH INSTITUTE AT NATIONWIDE CHILDREN S HOSPITAL   (United States)

^b UNIVERSITY OF PENNSYLVANIA   (United States)

^c UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^d UNIVERSITY OF MINNESOTA MEDICAL SCHOOL   (United States)

^e THE OHIO STATE UNIVERSITY COLLEGE OF MEDICINE   (United States)

^f CEDARS SINAI MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALLELE; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BETA THALASSEMIA; BLASTOCYST; CELL LINE; CONTROLLED STUDY; DIPLOIDY; DISEASE ASSOCIATION; EMBRYONIC STEM CELL; FEMALE; GAMETE; GENE TARGETING; GENE THERAPY; GENOME IMPRINTING; GENOTYPE PHENOTYPE CORRELATION; LOSS OF FUNCTION MUTATION; MOUSE; NONHUMAN; OOCYTE; PRIORITY JOURNAL; SPERM;

ALLELES; ANIMALS; BETA-THALASSEMIA; BLASTOCYST; CELL LINE; DISEASE MODELS, ANIMAL; EMBRYONIC STEM CELLS; GENE THERAPY; HUMANS; MICE; MICE, INBRED C57BL;

EID: 79551526508     PISSN: 00219738     EISSN: 15588238     Source Type: Journal    
DOI: 10.1172/JCI45377     Document Type: Article

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