Early versus late treatment of spinal cord compression with long-term intrathecal enzyme replacement therapy in canine mucopolysaccharidosis type I

Molecular Genetics and Metabolism

Volumn 101, Issue 2-3, 2010, Pages 115-122

  Dickson, Patricia I ^a   Hanson, Stephen ^b   McEntee, Michael F ^c   Vite, Charles H ^d   Vogler, Carole A ^e   Mlikotic, Anton ^a   Chen, Agnes H ^a   Ponder, Katherine P ^f   Haskins, Mark E ^d   Tippin, Brigette L ^a   Le, Steven Q ^a   Passage, Merry B ^a   Guerra, Catalina ^a   Dierenfeld, Ashley ^g   Jens, Jackie ^g   Snella, Elizabeth ^g   Kan, Shih hsin ^a   Ellinwood, N Matthew ^g  

^a HARBOR UCLA MEDICAL CENTER   (United States)

^b Veterinary Neurology Center   (United States)

^c UNIVERSITY OF TENNESSEE   (United States)

^d UNIVERSITY OF PENNSYLVANIA SCHOOL OF VETERINARY MEDICINE   (United States)

^e SAINT LOUIS UNIVERSITY SCHOOL OF MEDICINE   (United States)

^f WASHINGTON UNIVERSITY SCHOOL OF MEDICINE   (United States)

^g IOWA STATE UNIVERSITY   (United States)

Author keywords

Enzyme replacement therapy; Hurler; Intrathecal; Lysosomal storage disease; Mucopolysaccharidosis; Spinal cord compression

Indexed keywords

GLYCOSAMINOGLYCAN; LARONIDASE;

ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONTROLLED STUDY; DOG; ENZYME REPLACEMENT; INTERVERTEBRAL DISK; LONG TERM CARE; MENINX; MUCOPOLYSACCHARIDOSIS; NEUROLOGIC EXAMINATION; NONHUMAN; NUCLEAR MAGNETIC RESONANCE IMAGING; PRIORITY JOURNAL; SPINAL CORD COMPRESSION; SPINAL CORD VENTRAL HORN;

ANIMALS; DOGS; ENZYME REPLACEMENT THERAPY; HUMANS; IDURONIDASE; INJECTIONS, SPINAL; MAGNETIC RESONANCE IMAGING; MUCOPOLYSACCHARIDOSIS I; SPINAL CORD; SPINAL CORD COMPRESSION;

ANIMALIA; CANIS FAMILIARIS;

EID: 77957237019     PISSN: 10967192     EISSN: 10967206     Source Type: Journal    
DOI: 10.1016/j.ymgme.2010.06.020     Document Type: Article

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