Pathological evidence of Wolman's disease following hematopoietic stem cell transplantation despite correction of lysosomal acid lipase activity

Bone Marrow Transplantation

Volumn 44, Issue 7, 2009, Pages 449-450

  Gramatges, M M ^a   Dvorak, C C ^b   Regula, D P ^a   Enns, G M ^a   Weinberg, K ^a   Agarwal, R ^a  

^a STANFORD UNIVERSITY   (United States)

^b UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ACID LIPASE; ALEMTUZUMAB; BUSULFAN; FLUDARABINE; METHOTREXATE; TACROLIMUS;

ARTICLE; CASE REPORT; CAUSE OF DEATH; DIET SUPPLEMENTATION; ENZYME REPLACEMENT; FEMALE; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HISTOPATHOLOGY; HUMAN; HUMAN TISSUE; INFANT; LIVER DISEASE; LIVER FAILURE; MORTALITY; MULTIPLE ORGAN FAILURE; PARENTERAL NUTRITION; PRIORITY JOURNAL; REDUCED INTENSITY CONDITIONING; SEPSIS; SINUSOIDAL OBSTRUCTION SYNDROME; TREATMENT FAILURE; WOLMAN DISEASE;

FATAL OUTCOME; FEMALE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; INFANT; LIVER FAILURE; STEROL ESTERASE; TRANSPLANTATION CONDITIONING; WOLMAN DISEASE;

EID: 70350294674     PISSN: 02683369     EISSN: 14765365     Source Type: Journal    
DOI: 10.1038/bmt.2009.57     Document Type: Article

References (9)

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