Appraisal of the Pediatric Ulcerative Colitis Activity Index (PUCAI)

Inflammatory Bowel Diseases

Volumn 15, Issue 8, 2009, Pages 1218-1223

  Turner, Dan ^a,b   Hyams, Jeffrey ^c   Markowitz, James ^d   Lerer, Trudy ^c   Mack, David R ^e   Evans, Jonathan ^f   Pfefferkorn, Marian ^g   Rosh, Joel ^h   Kay, Marsha ⁱ   Crandall, Wallace ^j   Keljo, David ^k   Otley, Anthony R ^l   Kugathasan, Subra ^m   Carvalho, Ryan ⁿ   Oliva Hemker, Maria ^o   Langton, Christine ^c   Mamula, Petar ^p   Bousvaros, Athos ^q   LeLeiko, Neal ^r   Griffiths, Anne M ^b  

^a SHAARE ZEDEK MEDICAL CENTER   (Israel)

^b HOSPITAL FOR SICK CHILDREN   (Canada)

^c Farmington   (United States)

^d North Shore Long Island Jewish Health System ^*  (United States)

^e CHILDREN S HOSPITAL OF EASTERN ONTARIO   (Canada)

^f NEMOURS CHILDREN S CLINIC   (United States)

^g RILEY HOSPITAL FOR CHILDREN   (United States)

^h Goryeb Children's Hospital   (United States)

ⁱ LERNER RESEARCH INSTITUTE   (United States)

^j NATIONWIDE CHILDREN S HOSPITAL   (United States)

^k CHILDREN S HOSPITAL OF PITTSBURGH   (United States)

^l IWK HEALTH CENTRE   (Canada)

^m MEDICAL COLLEGE OF WISCONSIN   (United States)

ⁿ CHILDREN S MEDICAL CENTER   (United States)

^o JOHNS HOPKINS HOSPITAL   (United States)

^p CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^q BOSTON CHILDREN S HOSPITAL   (United States)

^r HASBRO CHILDREN'S HOSPITAL   (United States)

more..

Author keywords

Feasibility; Pediatrics; PUCAI; Responsiveness; Ulcerative colitis; Validity

Indexed keywords

6 MERCAPTOPURINE DERIVATIVE;

ADOLESCENT; ARTICLE; CHILD; COHORT ANALYSIS; DISEASE ACTIVITY; FEASIBILITY STUDY; FEMALE; FUNCTIONAL ASSESSMENT; HUMAN; MAJOR CLINICAL STUDY; MALE; OUTCOME ASSESSMENT; PEDIATRIC ULCERATIVE COLITIS ACTIVITY INDEX; PRIORITY JOURNAL; TEST RETEST RELIABILITY; ULCERATIVE COLITIS; VALIDITY;

ADOLESCENT; CHILD; CHILD, PRESCHOOL; COLITIS, ULCERATIVE; FEASIBILITY STUDIES; FEMALE; FOLLOW-UP STUDIES; HUMANS; INFANT; MALE; PREDICTIVE VALUE OF TESTS; PROSPECTIVE STUDIES; PSYCHOMETRICS; REGISTRIES; TREATMENT OUTCOME;

EID: 70349507127     PISSN: 10780998     EISSN: 15364844     Source Type: Journal    
DOI: 10.1002/ibd.20867     Document Type: Article

References (38)

1. Noble A, Turner D. Clinical outcomes in pediatric inflammatory bowel disease. In: Mamula P, Markowitz J, Baldassano R, eds. Springer, NY. Pediatric Inflammatory Bowel Disease, 1st ed. 2008. p 744.
2. Best WR, Becktel JM, Singleton JW, et al. Development of a Crohn's disease activity index. National Cooperative Crohn's Disease Study. Gastroenterology. 1976;70:439-444.
3. Hyams JS, Ferry GD, Mandel FS, et al. Development and validation of a pediatric Crohn's disease activity index. J Pediatr Gastroenterol Nutr. 1991;12:439-447.
4. D'Haens G, Sandborn WJ, Feagan BG, et al. A review of activity indices and efficacy end points for clinical trials of medical therapy in adults with ulcerative colitis. Gastroenterology. 2007;132:763-786.
5. Turner D, Otley AR, Mack D, et al. Development and evaluation of a Pediatric Ulcerative Colitis Activity Index (PUCAI): a prospective multicenter study. Gastroenterology. 2007;133:423-432.
6. Turner D, Walsh CM, Benchimol EI, et al. Severe paediatric ulcerative colitis: incidence, outcomes and optimal timing for second-line therapy. Gut. 2008;57:331-338.
7. McDowell I, Jenkinson C. Development standards for health measures. J Health Services Res Policy. 1996;1:238-246.
8. DeVellis RF. A consumer's guide to finding, evaluating, and reporting on measurement instruments. Arthritis Care Res. 1996;9:239-245.
9. Streiner D, Norman G. Validity. Health Measurement Scales. A Practical Guide to Their Development and Use, 2nd ed. Oxford: Oxford University Press; 1995.
10. Mack DR, Langton C, Markowitz J, et al. Laboratory values for children with newly diagnosed inflammatory bowel disease. Pediatrics. 2007; 119:1113-1119.
11. Shrout P, Fleiss J. Intraclass correlations: uses in assessing rater reliability. Psychol Bull. 1979;86:420-428.
12. Deyo RA, Centor RM. Assessing the responsiveness of functional scales to clinical change: an analogy to diagnostic test performance. J Chronic Dis. 1986;39:897-906.
13. Kundhal PS, Critch JN, Zachos M, et al. Pediatric Crohn Disease Activity Index: responsive to short-term change. J Pediatr Gastroenterol Nutr. 2003;36:83-89.
14. Liang MH, Fossel AH, Larson MG. Comparisons of five health status instruments for orthopedic evaluation. Med Care. 1990;28:632-642.
15. Stratford PW, Binkley FM, Riddle DL. Health status measures: strategies and analytic methods for assessing change scores. Phys Ther. 1996;76:1109-1123.
16. Guyatt G, Walter S, Norman G. Measuring change over time: assessing the usefulness of evaluative instruments. J Chronic Dis. 1987;40:171-178.
17. Jaeschke R, Singer J, Guyatt GH. Measurement of health status. Ascertaining the minimal clinically important difference. Control Clin Trials. 1989;10:407-415.
18. Schunemann HJ, Puhan M, Goldstein R, et al. Measurement properties and interpretability of the chronic respiratory disease questionnaire (CRQ). COPD. 2005;2:81-89.
19. Turner D, Schünemann HJ, Griffith LE, et al. Using the entire cohort in the ROC analysis maximizes precision of the minimal important difference. J Clin Epidemiol. 2008 (in press).
20. Hays RD, Woolley JM. The concept of clinically meaningful difference in health-related quality-of-life research. How meaningful is it? Pharmacoeconomics. 2000;18:419-423.
21. Beaton DE, Boers M, Wells GA. Many faces of the minimal clinically important difference (MCID): a literature review and directions for future research. Curr Opin Rheumatol. 2002;14:109-114.
22. Lassere MN, van der Heijde D, Johnson KR. Foundations of the minimal clinically important difference for imaging. J Rheumatol. 2001;28:890-891.
23. Lassere MN, van der Heijde D, Johnson K, et al. Robustness and generalizability of smallest detectable difference in radiological progression. J Rheumatol. 2001;28:911-913.
24. Beaton DE. Understanding the relevance of measured change through studies of responsiveness. Spine. 2000;25:3192-3199.
25. Jacobson NS, Truax P. Clinical significance: a statistical approach to defining meaningful change in psychotherapy research. J Consult Clin Psychol. 1991;59:12-19.
26. Jacobson NS, Roberts LJ, Berns SB, et al. Methods for defining and determining the clinical significance of treatment effects: description, application, and alternatives. J Consult Clin Psychol. 1999;67:300-307.
27. Turner D, Schünemann HJ, Griffith LE, et al. The minimal detectable change cannot reliably replace the minimal important difference. J Clin Epidemiol. 2008 (in press).
28. Wyrwich KW, Tierney WM, Wolinsky FD. Further evidence supporting an SEM-based criterion for identifying meaningful intra-individual changes in health-related quality of life. J Clin Epidemiol. 1999;52:861-873.
29. Wyrwich KW, Nienaber NA, Tierney WM, et al. Linking clinical relevance and statistical significance in evaluating intra-individual changes in health-related quality of life. Med Care. 1999;37:469-478.
30. Norman GR, Sloan JA, Wyrwich KW. Interpretation of changes in health-related quality of life: the remarkable universality of half a standard deviation. Med Care. 2003;41:582-592.
31. Crosby RD, Kolotkin RL, Williams GR. Defining clinically meaningful change in health-related quality of life. J Clin Epidemiol. 2003;56:395-407.
32. Norman GR, Stratford P, Regehr G. Methodological problems in the retrospective computation of responsiveness to change: the lesson of Cronbach. J Clin Epidemiol. 1997;50:869-879.
33. Wyrwich KW, Metz SM, Kroenke K, et al. Measuring patient and clinician perspectives to evaluate change in health-related quality of life among patients with chronic obstructive pulmonary disease. J Gen Intern Med. 2007;22:161-170.
34. Guyatt GH, Norman GR, Juniper EF, et al. A critical look at transition ratings. J Clin Epidemiol. 2002;55:900-908.
35. Cella D, Hahn EA, Dineen K. Meaningful change in cancer-specific quality of life scores: differences between improvement and worsening. Qual Life Res. 2002;11:207-221.
36. Irvine E. Assessing outcomes in clinical trials. In: Satsangi JSL, ed. Inflammatory Bowel Disease. Philadelphia: Churchill Livingstone; 2003. p 319-333.
37. Beattie RM, Nicholls SW, Domizio P, et al. Endoscopic assessment of the colonic response to corticosteroids in children with ulcerative colitis. J Pediatr Gastroenterol Nutr. 1996;22:373-379.
38. Silverberg MS, Satsangi J, Ahmad T, et al. Toward an integrated clinical, molecular and serological classification of inflammatory bowel disease: report of a Working Party of the 2005 Montreal World Congress of Gastroenterology. Can J Gastroenterol. 2005;19(suppl A):5-36.