Uptake of a recombinant human α-L-iduronidase (laronidase) by cultured fibroblasts and osteoblasts

Biological and Pharmaceutical Bulletin

Volumn 31, Issue 9, 2008, Pages 1691-1695

  Tsukimura, Takahiro ^a,b   Tajima, Youichi ^a   Kawashima, Ikuo ^a   Fukushige, Tomoko ^c   Kanzaki, Tamotsu ^c   Kanekura, Takuro ^c   Ikekita, Masahiko ^b   Sugawara, Kanako ^d   Suzuki, Toshihiro ^d   Togawa, Tadayasu ^d   Sakuraba, Hitoshi ^d  

^a TOKYO METROPOLITAN INSTITUTE OF MEDICAL SCIENCE   (Japan)

^b TOKYO UNIVERSITY OF SCIENCE   (Japan)

^c KAGOSHIMA UNIVERSITY   (Japan)

^d MEIJI PHARMACEUTICAL UNIVERSITY   (Japan)

Author keywords

L iduronidase; Enzyme replacement therapy; Mannose 6 phosphate receptor; Mucopolysaccharidosis I; Osteoblast

Indexed keywords

LARONIDASE; MANNOSE RECEPTOR; SOMATOMEDIN B RECEPTOR;

ANIMAL CELL; ARTICLE; CELL CULTURE; CONTROLLED STUDY; ENZYME REPLACEMENT; FIBROBLAST CULTURE; HUMAN; HUMAN CELL; HURLER SYNDROME; LYSOSOME; MOUSE; NONHUMAN; OSTEOBLAST; PROTEIN LOCALIZATION; PROTEIN TRANSPORT;

ANIMALS; CELLS, CULTURED; FIBROBLASTS; HUMANS; IDURONIDASE; KINETICS; MICE; MUCOPOLYSACCHARIDOSIS I; OSTEOBLASTS; RECEPTOR, IGF TYPE 2; RECOMBINANT PROTEINS;

EID: 51449120446     PISSN: 09186158     EISSN: 13475215     Source Type: Journal    
DOI: 10.1248/bpb.31.1691     Document Type: Article

References (11)

1. Neufeld E. F., Muenzer J., "The Metabolic and Molecular Bases of Inherited Disease," 8th ed., Vol. III, Chap. 136, ed. by Scriver C. R., Beaudet A. L., Sly W. S., Valle D., McGraw-Hill, New York, 2001, pp. 3421-3452.
2. Scott H. S., Ashton L. J., Eyre H. J., Baker E., Brooks D. A., Callen D. F., Sutherland G. R., Morris C. P., Hopwood J. J., Am. J. Hum. Genet., 47, 802-807 (1990).
3. Scott H. S., Anson D. S., Orsborn A. M., Nelson P. V., Clements P. R., Morris C. P., Hopwood J. J., Proc. Natl. Acad. Sci. U.S.A., 88, 9695-9699 (1991).
4. Kakkis E. D., Muenzer J., Tiller G. E., Waber L., Belmont J., Passage M., Izykowski B., Phillips J., Doroshow R., Walot I., Hoft R., Neufeld E. F., N. Engl. J. Med., 344, 182-188 (2001).
5. Wraith J. E., Clarke L. A., Beck M., Kolodny E. H., Pastores G. M., Muenzer J., Rapoport D. M., Berger K. I., Swiedler S. J., Kakkis E. D., Braakman T., Chadbourne E., Walton-Bowen K., Cox G. F., J. Pediatr., 144, 581-588 (2004).
6. Unger E. G., Durrant J., Anson D. S., Hopwood J. J., Biochem. J., 304, 43-49 (1994).
7. Hopwood J. J., Muller V., Smithson A., Baggett N., Clin. Chim. Acta, 92, 257-265 (1979).
8. Kanzaki T., Yokota M., Mizuno N., Matsumoto Y., Hirabayashi Y., Lancet, 1, 875-877 (1989).
9. Shull R. M., Kakkis E. D., McEntee M. F., Kania S. A., Jonas A. J., Neufeld E. F., Proc. Natl. Acad. Sci. U.S.A., 91, 12937-12941 (1994).
10. Kakkis E. D., McEntee M. F., Schmidtchen A., Neufeld E. F., Ward D. A., Gompf R. E., Kania S., Bedolla C., Chien S. L., Shull R. M., Biochem. Mol. Med., 58, 156-167 (1996).
11. Brooks D. A., Expert Opin. Biol. Ther., 2, 967-976 (2002).