Successful RPE65 gene replacement and improved visual function in humans

Ophthalmic Genetics

Volumn 29, Issue 3, 2008, Pages 89-91

  Koenekoop, Robert K ^a,b  

^a MCGILL UNIVERSITY   (Canada)

^b MONTREAL CHILDREN S HOSPITAL   (Canada)

Author keywords

Blindness; Gene therapy; LCA; RPE65

Indexed keywords

PREDNISONE;

GENE; GENE REPLACEMENT THERAPY; GENETIC ASSOCIATION; HUMAN; INFLAMMATION; LEBER CONGENITAL AMAUROSIS; NONHUMAN; PRIORITY JOURNAL; REVIEW; RPE65 GENE; VISION; VISUAL ACUITY; VISUAL FIELD;

ANIMALS; BLINDNESS; CARRIER PROTEINS; EYE PROTEINS; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENES, RECESSIVE; HUMANS; RETINAL DEGENERATION;

MUS;

EID: 51049087941     PISSN: 13816810     EISSN: 17445094     Source Type: Journal    
DOI: 10.1080/13816810802216480     Document Type: Review

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