Stem cell transplantation for primary immunodeficiencies

Bone Marrow Transplantation

Volumn 41, Issue SUPPL. 2, 2008, Pages

  Porta, F ^a   Forino, C ^a   De Martiis, D ^a   Soncini, E ^a   Notarangelo, L ^a   Tettoni, K ^a   D'Ippolito, C ^a   Soresina, R ^a   Shiha, K ^a   Berta, S ^a   Baffelli, R ^a   Bolda, F ^a   Bosi, A ^a   Schumacher, F R ^a   Lanfranchi, A ^a   Mazzolari, E ^a  

^a Ospedale dei Bambini   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

ALLOGENEIC STEM CELL TRANSPLANTATION; ARTICLE; BONE MARROW TRANSPLANTATION; CELL FUNCTION; CHILD; DISEASE SEVERITY; DONOR SELECTION; ENGRAFTMENT; ENZYME THERAPY; GENE THERAPY; GRAFT SURVIVAL; HUMAN; IMMUNE DEFICIENCY; LIFE EXPECTANCY; LYMPHOCYTE FUNCTION; NATURAL KILLER CELL; PRIORITY JOURNAL; QUALITY OF LIFE; SEVERE COMBINED IMMUNODEFICIENCY; STEM CELL TRANSPLANTATION; SURVIVAL RATE; T LYMPHOCYTE; TREATMENT INDICATION; TREATMENT RESPONSE;

BONE MARROW TRANSPLANTATION; CHILD, PRESCHOOL; DISEASE-FREE SURVIVAL; HUMANS; IMMUNOLOGIC DEFICIENCY SYNDROMES; INFANT; ITALY; REGISTRIES; STEM CELL TRANSPLANTATION; TRANSPLANTATION, HOMOLOGOUS;

EID: 45749129127     PISSN: 02683369     EISSN: 14765365     Source Type: Journal    
DOI: 10.1038/bmt.2008.61     Document Type: Article

References (10)

1. Porta F, Friedrich W. Bone marrow transplantation in congenital immunodeficiency diseases. Bone Marrow Transplant 1998; 21 (Suppl 2): S21-S23. Review.
2. Bertand Y, Landais P, Friedrich W, Gerritsen B, Morgan G. Fasth A et al. Influence of severe combined immunodeficiency phenotype on the outcorne of HLA non-identical, T-cell-depleted bone marrow transplantation: A retrospective European survey from the European group for blood and marrow transplantation and the European society for immunodeficiency. J Pediatr 1999; 134: 740-748.
3. Lanfranchi A, Verardi R, Tettoni K, Neva A, Mazzolari E. Pennacchi M et al. Haploidentical peripheral blood and marrow stem cell transplantation in nine cases of primary immunodeficiency. Haematologica 2000; 85: 41-46.
4. Seger RA, Gungor T, Belohradsky BH, Blanche S, Bordigoni P, Di Bartolomeo P et al. Treatment of chronic granulomatous disease with myeloablative conditioning and an unmodified hemopoietic allograft: a survey of the European experience. 1985-2000. Blood 2002: 100 4344-4350. Review.
5. Driesse GJ, Gerritsen EJ, Fischer A, Fasth A, Hop WC, Veys P et al Long-term outcome of haematopoietic stem cell transplantation in autosomal recessive osteopetrosis: An EBMT report. Bone Marrow Transplant 2003; 32: 657-663.
6. Bartolome J, Porta F, Lanfranchi A, Rodriguez-Molina JJ, Cela E, Cantalejo A et al. B cell function after haploidentical in utero bone marrow transplantation in a patient with severe combined immunodeficiency. Bone Marrow Transplant 2002; 29: 625-628.
7. Pirovano S, Notarangelo LD, Malacarne F, Mazzolari E, Porta F. Lanfranchi A el al. Reconstitution of T-cell compartment after in utero stem cell transplantation: Analysis of T-cell repertoire and thymic output. Haematologica 2004: 89: 450-461.
8. Mazzolari E, Moshous D, Forino C, De Martiis D, Offer C. Lanfranchi A et al. Hematopoietic stem cell transplantation in Omenn syndrome: A single-center experience. Bone Marrow Transplant 2005: 36: 107-114.
9. Grunebaum E, Mazzolari E, Porta F, Dallera D, Atkinson A, Reid B et al. Bone marrow transplantation for severe combined immune deficiency. JAMA 2006; 295: 508-518.
10. Pai SY, DeMartiis D, Forino C, Cavagnini S, Lanfranchi A, Giliani S et al. Stem cell transplantation for the Wiskott-Aldrich Syndrome: A single-centre experience confirms efficacy of matched unrelated transplantation. Bone Marrow Transplant 2006; 38: 671-679.