Hematopoietic stem cell transplantation in Omenn syndrome: A single-center experience

Bone Marrow Transplantation

Volumn 36, Issue 2, 2005, Pages 107-114

  Mazzorali, E ^a   Moshous, D ^a   Forino, C ^a   De Martiis, D ^a   Offer, C ^a   Lanfranchi, A ^a   Giliani, S ^a   Imberti, L ^b   Pasic, S ^c   Ugazio, A G ^a,d   Porta, F ^a   Notarangelo, L D ^a  

^a UNIVERSITY OF BRESCIA   (Italy)

^b Laboratorio di Biotecnologie   (Serbia)

^c Mother and Child's Institute   (Serbia)

^d Ospedale Pediatrico Bambino Gesù   (Serbia)

Author keywords

Omenn syndrome; Severe Combined Immunodeficiency; Stem cell transplantation

Indexed keywords

ALEMTUZUMAB; ANTIBIOTIC AGENT; ANTIFUNGAL AGENT; ANTIVIRUS AGENT; BUSULFAN; CD16 ANTIGEN; CD19 ANTIGEN; CD3 ANTIGEN; CD4 ANTIGEN; CD8 ANTIGEN; CYCLOPHOSPHAMIDE; CYCLOSPORIN A; ETOPOSIDE; FLUDARABINE; GRANULOCYTE COLONY STIMULATING FACTOR; HLA ANTIGEN; IMMUNOGLOBULIN A; IMMUNOGLOBULIN E; IMMUNOGLOBULIN G; IMMUNOGLOBULIN M; MELPHALAN; OKT 3; RAG1 PROTEIN; RAG2 PROTEIN; STEROID; THIOTEPA; THYMOCYTE ANTIBODY;

ANTIBODY PRODUCTION; ARTICLE; AUTOIMMUNITY; CLINICAL ARTICLE; COMBINED IMMUNODEFICIENCY; CONTROLLED STUDY; DONOR; EXPERIENCE; GENE MUTATION; GENETIC ANALYSIS; GRAFT INFECTION; GRAFT SURVIVAL; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOLYTIC ANEMIA; HLA MATCHING; HUMAN; HUMAN CELL; HYPOTHYROIDISM; IDIOPATHIC THROMBOCYTOPENIC PURPURA; INFANT; LEUKAPHERESIS; LYMPHOCYTE FUNCTION; MEDICAL ASSESSMENT; MORTALITY; MYASTHENIA GRAVIS; OMENN SYNDROME; PHENOTYPE; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; RETROSPECTIVE STUDY; STEM CELL MOBILIZATION; SURVIVAL; T CELL DEPLETION; T LYMPHOCYTE; TIME; TREATMENT OUTCOME;

EID: 22744449873     PISSN: 02683369     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.bmt.1705017     Document Type: Article

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