Progress reported in two studies of clinical gene transfer into the retina

Molecular Therapy

Volumn 16, Issue 7, 2008, Pages 1181-

  Williams, David A ^a  

^a NONE

Author keywords

[No Author keywords available]

Indexed keywords

BETA ACTIN; COMPLEMENTARY DNA; PARVOVIRUS VECTOR; RETINAL PIGMENT EPITHELIUM SPECIFIC PROTEIN 65; VISUAL PIGMENT;

EDITORIAL; EXPRESSION VECTOR; GENE MUTATION; GENE TRANSFER; HUMAN; LEBER CONGENITAL AMAUROSIS; NONHUMAN; PROMOTER REGION; RETINA DEGENERATION; RISK FACTOR; TREATMENT RESPONSE; VIRAL GENE DELIVERY SYSTEM; VIRUS PARTICLE; VISUAL ACUITY; VISUAL FIELD;

EID: 45749113738     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2008.123     Document Type: Editorial

References (2)

1. Bainbridge, JW, Smith, AJ, Barker, SS, Robbie, S, Henderson, R, Balaggan, K et al. (2008). Effect of gene therapy on visual function in Leber's congenital amaurosis. N Engl J Med; e-pub ahead of print 27 April 2008.
2. Maguire, AM, Simonelli, F, Pierce, EA, Pugh, EN Jr, Mingozzi, F, Bennicelli, J et al. (2008). Safety and efficacy of gene transfer for Leber's congenital amaurosis. N Engl J Med; e-pub ahead of print 28 April 2008.