Rare diseases: what's next?

The Lancet

Volumn 371, Issue 9629, 2008, Pages 1978-1979

  Remuzzi, Giuseppe ^a   Garattini, Silvio ^a  

^a MARIO NEGRI INST PHARMACOL RES   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

AGALSIDASE BETA; ARSENIC TRIOXIDE; IMATINIB; ORPHAN DRUG;

ARTICLE; CHRONIC MYELOID LEUKEMIA; DISEASE REGISTRY; DRUG APPROVAL; DRUG COST; FABRY DISEASE; FUNDING; GASTROINTESTINAL STROMAL TUMOR; GENE THERAPY; HEALTH CARE PLANNING; HEALTH CARE POLICY; HUMAN; POLITICAL PARTICIPATION; PREVALENCE; PRIORITY JOURNAL; PROMYELOCYTIC LEUKEMIA; RARE DISEASE;

EID: 44849113819     PISSN: 01406736     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0140-6736(08)60847-8     Document Type: Note

References (11)

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