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Volumn 358, Issue 21, 2008, Pages 2282-2284

Preliminary results of gene therapy for retinal degeneration

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; COMPLEMENTARY DNA; CORTICOSTEROID; RETINAL PIGMENT EPITHELIUM SPECIFIC PROTEIN;

EID: 44249100641     PISSN: 00284793     EISSN: 15334406     Source Type: Journal    
DOI: 10.1056/NEJMe0803081     Document Type: Editorial
Times cited : (24)

References (10)
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    • Bainbridge, JWB1    Smith, AJ2    Barker, SS3
  • 2
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    • Safety and efficacy of gene transfer for Leber's congenital amaurosis.
    • AM Maguire F Simonelli EA Pierce Safety and efficacy of gene transfer for Leber's congenital amaurosis. N Engl J Med 358 2008 2240 2248
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    • Maguire, AM1    Simonelli, F2    Pierce, EA3
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    • Leber congenital amaurosis: comprehenseive survey of the genetic heterogeneity, refinement of the clinical definition, and genotype-phenotype correlations as a strategy for molecular diagnosis.
    • S Hanein I Perrault S Gerber Leber congenital amaurosis: comprehenseive survey of the genetic heterogeneity, refinement of the clinical definition, and genotype-phenotype correlations as a strategy for molecular diagnosis. Hum Mutat 23 2004 306 317
    • (2004) Hum Mutat , vol.23 , pp. 306-317
    • Hanein, S1    Perrault, I2    Gerber, S3
  • 5
    • 38549098447 scopus 로고    scopus 로고
    • Leber congenital amaurosis: disease, genetics and therapy.
    • E Ahmed J Loewenstein Leber congenital amaurosis: disease, genetics and therapy. Semin Ophthalmol 23 2008 39 43
    • (2008) Semin Ophthalmol , vol.23 , pp. 39-43
    • Ahmed, E1    Loewenstein, J2
  • 6
    • 0031255068 scopus 로고    scopus 로고
    • Mutations in RPE65 cause autosomal recessive childhood-onset severe retinal dystrophy.
    • S-M Gu DA Thompson CRS Srikumari Mutations in RPE65 cause autosomal recessive childhood-onset severe retinal dystrophy. Nat Genet 17 1997 194 197
    • (1997) Nat Genet , vol.17 , pp. 194-197
    • Gu, S-M1    Thompson, DA2    Srikumari, CRS3
  • 7
    • 28444442243 scopus 로고    scopus 로고
    • Long-term restoration of rod and cone vision by single dose rAAV-mediated gene transfer to the retina in a canine model of childhood blindness.
    • GM Acland GD Aguirre J Bennett Long-term restoration of rod and cone vision by single dose rAAV-mediated gene transfer to the retina in a canine model of childhood blindness. Mol Ther 12 2005 1072 1082
    • (2005) Mol Ther , vol.12 , pp. 1072-1082
    • Acland, GM1    Aguirre, GD2    Bennett, J3
  • 8
    • 39849110435 scopus 로고    scopus 로고
    • Reversal of blindness in animal models of Leber congenital amaurosis using optimized AAV2-mediated gene transfer.
    • J Bennicelli JF Wright A Komaromy Reversal of blindness in animal models of Leber congenital amaurosis using optimized AAV2-mediated gene transfer. Mol Ther 16 2008 458 465
    • (2008) Mol Ther , vol.16 , pp. 458-465
    • Bennicelli, J1    Wright, JF2    Komaromy, A3
  • 9
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    • Impairment of the transient papillary light reflex in Rpe65(−/−) mice and humans with Leber congenital amaurosis.
    • TS Aleman SG Jacobson JD Chico Impairment of the transient papillary light reflex in Rpe65(−/−) mice and humans with Leber congenital amaurosis. Invest Ophthalmol Vis Sci 45 2004 1259 1271
    • (2004) Invest Ophthalmol Vis Sci , vol.45 , pp. 1259-1271
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  • 10
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    • Correlation of pathologic features in spectral domain optical coherence tomography with conventional retinal studies.
    • M Stopa BA Bower E Davies JA Izatt CA Toth Correlation of pathologic features in spectral domain optical coherence tomography with conventional retinal studies. Retina 28 2008 298 308
    • (2008) Retina , vol.28 , pp. 298-308
    • Stopa, M1    Bower, BA2    Davies, E3    Izatt, JA4    Toth, CA5


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.