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Volumn 1, Issue 6, 2006, Pages 521-524

The impact of the Orphan Drug Act on drug discovery

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EID: 41049098130     PISSN: 17460441     EISSN: 1746045X     Source Type: Journal    
DOI: 10.1517/17460441.1.6.521     Document Type: Review
Times cited : (9)

References (22)
  • 1
    • 80052573662 scopus 로고    scopus 로고
    • Pushing parentless pharmaceuticals: Toward an international home for orphan drugs and a cure for zebra diseases
    • CAVALIER GM: Pushing parentless pharmaceuticals: toward an international home for orphan drugs and a cure for zebra diseases. Law Policy Int. Bus. (1996) 27:447-476.
    • (1996) Law Policy Int. Bus. , vol.27 , pp. 447-476
    • Cavalier, G.M.1
  • 2
    • 1542543205 scopus 로고    scopus 로고
    • Orphan products: Hope for people with rare diseases
    • Nov-Dec
    • RADOS C: Orphan products: hope for people with rare diseases. FDA Consumer Magazine. Nov-Dec (2003).
    • (2003) FDA Consumer Magazine
    • Rados, C.1
  • 4
    • 0023146216 scopus 로고
    • Treatement of adenosine demainase deficincy with polyethylene glycol modified adenosine deaminase
    • HERSHFIELD MS, BUCKLEY RH, GREENBERG ML et al.: Treatement of adenosine demainase deficincy with polyethylene glycol modified adenosine deaminase. N. Engl. J. Med. (1987) 316:589-596.
    • (1987) N. Engl. J. Med. , vol.316 , pp. 589-596
    • Hershfield, M.S.1    Buckley, R.H.2    Greenberg, M.L.3
  • 5
    • 0037837490 scopus 로고    scopus 로고
    • The Orphan Drug backlash
    • MAEDER T: The Orphan Drug backlash. Sci. Am. (2003) 288(5):80.
    • (2003) Sci. Am. , vol.288 , Issue.5 , pp. 80
    • Maeder, T.1
  • 6
    • 0029644362 scopus 로고
    • Elixirs, diluents and the passage of the 1938 federal food, drug and cosmetic act
    • WAX PM: Elixirs, diluents and the passage of the 1938 federal food, drug and cosmetic act. Ann. Intern. Med. (1995) 122(6):456-461.
    • (1995) Ann. Intern. Med. , vol.122 , Issue.6 , pp. 456-461
    • Wax, P.M.1
  • 9
    • 33646264593 scopus 로고
    • Imuune response to polyethylene glycol modified bovine adenosine deaminase (PEG-ADA)
    • CHAFFEE S, HERSFIELD MS: Imuune response to polyethylene glycol modified bovine adenosine deaminase (PEG-ADA). Pediatr Res. (1990) 27(4 Pt 2):155A.
    • (1990) Pediatr Res. , vol.27 , Issue.4 PART 2
    • Chaffee, S.1    Hersfield, M.S.2
  • 12
    • 1842586020 scopus 로고    scopus 로고
    • Premature stop codons involved in muscular dystrophies show a broad spectrum of read through efficiencies in response to gentamicin treatment
    • BIDOU L, HATIN I, PEREZ N, ALLAMAND V, PANTHIER JJ, ROUSSET JP: Premature stop codons involved in muscular dystrophies show a broad spectrum of read through efficiencies in response to gentamicin treatment. Gene Ther. (2004) 11:619-267.
    • (2004) Gene Ther. , vol.11 , pp. 619-267
    • Bidou, L.1    Hatin, I.2    Perez, N.3    Allamand, V.4    Panthier, J.J.5    Rousset, J.P.6
  • 13
    • 23044440450 scopus 로고    scopus 로고
    • The impact of CYP2C9 and VKORC1 genetic polymorphism and patient characteristics upon warfarin dose requirements: Proposal for a new dosing regime
    • SCONE EA, KHAN TI, WYNNE HA et al.: The impact of CYP2C9 and VKORC1 genetic polymorphism and patient characteristics upon warfarin dose requirements: proposal for a new dosing regime. Blood (2005) 106:2329-2333.
    • (2005) Blood , vol.106 , pp. 2329-2333
    • Scone, E.A.1    Khan, T.I.2    Wynne, H.A.3
  • 14
    • 80052605479 scopus 로고    scopus 로고
    • OOPD Grant no. FDR-000285-01 to ABUCHOWSKI A. Severe combined immunogenicity disease: enzyme therapy. Rockville (MD)
    • http://www.fda.gov/orphan/grants/previous. htm OOPD. Grant no. FDR-000285-01 to ABUCHOWSKI A. Severe combined immunogenicity disease: enzyme therapy. Rockville (MD).
  • 18
    • 85037323287 scopus 로고    scopus 로고
    • CFR 21 Part 316. Docket No. 85N-0483
    • http://www.fda.gov/Cber/gdlns/orphan.htm The Orphan Drug Regulations. CFR 21 Part 316. Docket No. 85N-0483.
    • The Orphan Drug Regulations
  • 19
    • 80052577636 scopus 로고    scopus 로고
    • From orphan to blockbuster? Biotechs lead the way in getting orphan drugs to market, and sometimes they actually make money
    • http://money.cnn.com/2005/07/08/news/midcaps/orphan/index.htm SMITH A: From orphan to blockbuster? Biotechs lead the way in getting orphan drugs to market, and sometimes they actually make money. CNN Money.
    • CNN Money
    • Smith, A.1
  • 22
    • 80052577350 scopus 로고    scopus 로고
    • Institute for One World Health
    • http://www.oneworldhealth.org/business/index.php Institute for One World Health.


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.