Functional recovery in a Friedreich's ataxia mouse model by frataxin gene transfer using an HSV-1 amplicon vector

Molecular Therapy

Volumn 15, Issue 6, 2007, Pages 1072-1078

  Lim, Filip ^a   Palomo, Gloria M ^a   Mauritz, Christina ^a   Giménez Cassina, Alfredo ^a   Illana, Belen ^a   Wandosell, Francisco ^a   Díaz Nido, Javier ^a  

^a UNIVERSIDAD AUTÓNOMA DE MADRID   (Spain)

Author keywords

[No Author keywords available]

Indexed keywords

FRATAXIN; HERPESVIRUS VECTOR;

AMPLICON; ANIMAL BEHAVIOR; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BRAIN NERVE CELL; CONTROLLED STUDY; DRUG MECHANISM; EMBRYO; FEMALE; FRIEDREICH ATAXIA; GENE EXPRESSION; GENE TRANSFER; HERPES SIMPLEX VIRUS 1; IN VIVO STUDY; KNOCKOUT MOUSE; LOW DRUG DOSE; LOXP SITE; MOUSE; NONHUMAN; ROTAROD TEST; TRANSGENIC MOUSE; VIRAL GENE THERAPY;

ANIMALS; BLOTTING, WESTERN; BRAIN STEM; CELLS, CULTURED; DISEASE MODELS, ANIMAL; FEMALE; FRIEDREICH ATAXIA; GENE AMPLIFICATION; GENE LIBRARY; GENETIC VECTORS; HERPESVIRUS 1, HUMAN; HUMANS; IRON-BINDING PROTEINS; MICE; MICE, KNOCKOUT; MICE, TRANSGENIC; MUTATION; NEURONS; ROTAROD PERFORMANCE TEST;

ANIMALIA; HUMAN HERPESVIRUS 1; MUS; MUS MUSCULUS;

EID: 34249334648     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/sj.mt.6300143     Document Type: Article

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