Bone marrow transplantation for feline mucopolysaccharidosis I

Molecular Genetics and Metabolism

Volumn 91, Issue 3, 2007, Pages 239-250

  Ellinwood, N Matthew ^a   Colle, Marie Anne ^b   Weil, Margaret A ^a   Casal, Margret L ^a   Vite, Charles H ^a   Wiemelt, Staci ^a   Hasson, Christopher W ^a   O'Malley, Thomas M ^a   He, Xingxuan ^c   Prociuk, Ulana ^a   Verot, Lucie ^d   Melniczek, John R ^a   Lannon, Anne ^a   Aguirre, Gustavo D ^a   Knox, Van W ^a   Evans, Sydney M ^a   Vanier, Marie T ^d   Schuchman, Edward H ^c   Walkley, Steven U ^e   Haskins, Mark E ^a  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b INRA UMR 703   (France)

^c MOUNT SINAI SCHOOL OF MEDICINE   (United States)

^d INSERM   (France)

^e New York State Office of Mental Retardation and Developmental Disabilities   (United States)

Author keywords

Bone marrow transplantation; Disease models, animal; Glycosaminoglycans; Iduronidase; Lysosomal storage diseases; Mucopolysaccharidosis I

Indexed keywords

GANGLIOSIDE; GLYCOSAMINOGLYCAN; LEVO IDURONIDASE;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; AORTA; ARTICLE; BONE MARROW TRANSPLANTATION; BRAIN LEVEL; CAT; CERVICAL SPINE; CERVICAL SPINE RADIOGRAPHY; CONTROLLED STUDY; ENZYME ACTIVITY; FEMALE; HEART MUSCLE; IMMUNOHISTOCHEMISTRY; KIDNEY; LIVER; LUNG; MALE; MUCOPOLYSACCHARIDOSIS; NONHUMAN; PELVIS RADIOGRAPHY; PRIORITY JOURNAL; SPLEEN; THYROID GLAND;

ANIMALS; BONE MARROW TRANSPLANTATION; CATS; FEMALE; GANGLIOSIDES; GLYCOSAMINOGLYCANS; HETEROZYGOTE; IDURONIDASE; MALE; MUCOPOLYSACCHARIDOSIS I; ORGAN SPECIFICITY;

ANIMALIA; FELIDAE;

EID: 34249305165     PISSN: 10967192     EISSN: 10967206     Source Type: Journal    
DOI: 10.1016/j.ymgme.2007.03.001     Document Type: Article

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