Sequence-specific modification of a β-thalassemia locus by small DNA fragments in human erythroid progenitor cells

Haematologica

Volumn 92, Issue 1, 2007, Pages 129-130

  Colosimo, Alessia ^a,b,c   Guida, Valentina ^a,b,d   Antonucci, Ivana ^e   Bonfini, Tiziana ^f   Stuppia, Liborio ^e   Dallapiccola, Bruno ^a,b,d  

^a IRCCS CSS San Giovanni Rotondo   (Italy)

^b CASA SOLLIEVO DELLA SOFFERENZA HOSPITAL   (Italy)

^c UNIVERSITY OF TERAMO   (Italy)

^d SAPIENZA UNIVERSITY OF ROME   (Italy)

^e UNIVERSITY OF CHIETI   (Italy)

^f ASL Pescara   (Italy)

Author keywords

thalassemia; Gene targeting; Gene therapy; HBB gene

Indexed keywords

BETA GLOBIN; DNA FRAGMENT; MESSENGER RNA;

AMINO ACID SUBSTITUTION; ARTICLE; BETA THALASSEMIA; CODON; DRUG MECHANISM; ERYTHROID PRECURSOR CELL; GENE LOCUS; GENE MUTATION; GENE SEQUENCE; GENE TARGETING; HUMAN; POLYMERASE CHAIN REACTION; RESTRICTION FRAGMENT LENGTH POLYMORPHISM;

ALLELES; BASE SEQUENCE; BETA-THALASSEMIA; CODON; DNA FRAGMENTATION; ELECTROPORATION; ERYTHROID PROGENITOR CELLS; GENE TARGETING; GLOBINS; HETEROZYGOTE; HUMANS; MOLECULAR SEQUENCE DATA; MUTATION; POLYMERASE CHAIN REACTION; RNA, MESSENGER;

EID: 33846923834     PISSN: 03906078     EISSN: None     Source Type: Journal    
DOI: 10.3324/haematol.10560     Document Type: Article

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