Glucose-6-phosphate transporter gene therapy corrects metabolic and myeloid abnormalities in glycogen storage disease type Ib mice

Gene Therapy

Volumn 14, Issue 3, 2007, Pages 219-226

  Yiu, W H ^a   Pan, C J ^a   Allamarvdasht, M ^a   Kim, S Y ^a   Chou, J Y ^a  

^a EUNICE KENNEDY SHRIVER NATIONAL INSTITUTE OF CHILD HEALTH AND HUMAN DEVELOPMENT   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; CARRIER PROTEIN; CHOLESTEROL; COLONY STIMULATING FACTOR 1; GLUCOSE; GLUCOSE 6 PHOSPHATE TRANSPORTER; GLYCOGEN; GRANULOCYTE COLONY STIMULATING FACTOR; GRANULOCYTE MACROPHAGE COLONY STIMULATING FACTOR; LACTIC ACID; MEMBRANE PROTEIN; MESSENGER RNA; TRIACYLGLYCEROL; UNCLASSIFIED DRUG; URIC ACID;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BONE DEVELOPMENT; BONE MARROW; BONE MARROW DISEASE; CELLULAR DISTRIBUTION; CHOLESTEROL BLOOD LEVEL; CONTROLLED STUDY; DRUG USE; ENDOPLASMIC RETICULUM; FEASIBILITY STUDY; GENE EXPRESSION; GENE REPLACEMENT THERAPY; GLUCOSE BLOOD LEVEL; GLUCOSE HOMEOSTASIS; GLYCOGEN LIVER LEVEL; GLYCOGEN STORAGE DISEASE TYPE 1; GLYCOGEN STORAGE DISEASE TYPE 1B; GROWTH CURVE; HEMATOPOIETIC STEM CELL; LACTATE BLOOD LEVEL; LIVER; METABOLIC DISORDER; MOUSE; NEUTROPENIA; NONHUMAN; NUCLEOTIDE SEQUENCE; PRIORITY JOURNAL; PROTEIN BLOOD LEVEL; SPLEEN; TRIACYLGLYCEROL BLOOD LEVEL; URIC ACID BLOOD LEVEL; VIRAL GENE DELIVERY SYSTEM;

ADENOVIRIDAE; ANIMALS; ANIMALS, NEWBORN; BONE MARROW; GENE EXPRESSION; GENE THERAPY; GENETIC VECTORS; GLUCOSE TRANSPORT PROTEINS, FACILITATIVE; GLUCOSE-6-PHOSPHATE; GLYCOGEN STORAGE DISEASE TYPE I; HUMANS; INJECTIONS; MICE; MICE, KNOCKOUT; MICROSOMES, LIVER; NEUTROPENIA; SPLEEN; TRANSDUCTION, GENETIC; TRANSGENES;

MUS;

EID: 33846488084     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/sj.gt.3302869     Document Type: Article

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