-
1
-
-
26844545020
-
Animal models for growth hormone gene therapy
-
Peroni, C. N., Gout, P. W., and Bartolini, P. (2005) Animal models for growth hormone gene therapy. Curr. Gene Ther. 5, 493-509.
-
(2005)
Curr. Gene Ther
, vol.5
, pp. 493-509
-
-
Peroni, C.N.1
Gout, P.W.2
Bartolini, P.3
-
2
-
-
0024988334
-
Gene transfer into humans: Immunotherapy of patients with advanced melanoma, using tumor-infiltrating lymphocytes modified by retroviral gene transduction
-
Rosenberg, S. A., Aebersold, P., Cornetta, K., et al. (1990) Gene transfer into humans: immunotherapy of patients with advanced melanoma, using tumor-infiltrating lymphocytes modified by retroviral gene transduction. N. Engl. J. Med. 323, 570-578.
-
(1990)
N. Engl. J. Med
, vol.323
, pp. 570-578
-
-
Rosenberg, S.A.1
Aebersold, P.2
Cornetta, K.3
-
3
-
-
4444370799
-
Gene therapy clinical trials worldwide 1989-2004: An overview
-
Edelstein, M. L., Abedi, M. R., Wixon, J., and Edelstein, R. M. (2004) Gene therapy clinical trials worldwide 1989-2004: an overview. J. Gene Med. 6, 597-602.
-
(2004)
J. Gene Med
, vol.6
, pp. 597-602
-
-
Edelstein, M.L.1
Abedi, M.R.2
Wixon, J.3
Edelstein, R.M.4
-
5
-
-
1542319138
-
The future of gene therapy
-
Cavazzana-Calvo, M., Thrasher, A., and Mavilio, F. (2004) The future of gene therapy. Nature 427, 779-781.
-
(2004)
Nature
, vol.427
, pp. 779-781
-
-
Cavazzana-Calvo, M.1
Thrasher, A.2
Mavilio, F.3
-
6
-
-
0034724857
-
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
-
Cavazzana-Calvo, M., Hacein-Bey, S., de Saint Basile, G., et al. (2000) Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease. Science 288, 669-672.
-
(2000)
Science
, vol.288
, pp. 669-672
-
-
Cavazzana-Calvo, M.1
Hacein-Bey, S.2
de Saint Basile, G.3
-
7
-
-
18444376150
-
Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement
-
Aiuti, A., Vai, S., Mortellaro, A., et al. (2002) Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement. Nat. Med. 8, 423-425.
-
(2002)
Nat. Med
, vol.8
, pp. 423-425
-
-
Aiuti, A.1
Vai, S.2
Mortellaro, A.3
-
8
-
-
0037189401
-
Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning
-
Aiuti, A., Slavin, S., Aker, M., et al. (2002) Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning. Science 296, 2410-2413.
-
(2002)
Science
, vol.296
, pp. 2410-2413
-
-
Aiuti, A.1
Slavin, S.2
Aker, M.3
-
9
-
-
0037448352
-
A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency
-
Hacein-Bey-Abina, S., von Kalle, C., Schmidt, M., et al. (2003) A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency. N. Engl. J. Med. 348, 255-256.
-
(2003)
N. Engl. J. Med
, vol.348
, pp. 255-256
-
-
Hacein-Bey-Abina, S.1
von Kalle, C.2
Schmidt, M.3
-
10
-
-
0142084745
-
LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1
-
Hacein-Bey-Abina, S., von Kalle, C., Schmidt, M., et al. (2003) LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1. Science 302, 415-419.
-
(2003)
Science
, vol.302
, pp. 415-419
-
-
Hacein-Bey-Abina, S.1
von Kalle, C.2
Schmidt, M.3
-
11
-
-
0142089747
-
Fatal systemic inflammatory response syndrome in an ornithine transcarbamylase deficient patient following adenoviral gene transfer
-
Raper, S. E., Chirmule, N., Lee, F. S., et al. (2003) Fatal systemic inflammatory response syndrome in an ornithine transcarbamylase deficient patient following adenoviral gene transfer. Mol. Genet. Metab. 80, 148-158.
-
(2003)
Mol. Genet. Metab
, vol.80
, pp. 148-158
-
-
Raper, S.E.1
Chirmule, N.2
Lee, F.S.3
-
13
-
-
0028153271
-
Long-term production and delivery of human growth hormone in vivo
-
Heartlein, M. W., Roman, V. A., Jiang, J., et al. (1994) Long-term production and delivery of human growth hormone in vivo. Proc. Natl. Acad. Sci. USA 91, 10,967-10,971.
-
(1994)
Proc. Natl. Acad. Sci. USA
, vol.91
-
-
Heartlein, M.W.1
Roman, V.A.2
Jiang, J.3
-
14
-
-
0031952892
-
Systemic action of human growth hormone following adenovirus-mediated gene transfer to rat submandibular glands
-
He, X., Goldsmith, C. M., Marmary, Y., et al. (1998) Systemic action of human growth hormone following adenovirus-mediated gene transfer to rat submandibular glands. Gene Ther. 5, 537-541.
-
(1998)
Gene Ther
, vol.5
, pp. 537-541
-
-
He, X.1
Goldsmith, C.M.2
Marmary, Y.3
-
15
-
-
0642303112
-
Increases in weight of growth hormone-deficient and immunodeficient (lit/scid) dwarf mice after grafting of hGH-secreting, primary human keratinocytes
-
Bellini, M. H., Peroni, C. N., and Bartolini P. (2003) Increases in weight of growth hormone-deficient and immunodeficient (lit/scid) dwarf mice after grafting of hGH-secreting, primary human keratinocytes. FASEB J. 17, 2322-2324.
-
(2003)
FASEB J
, vol.17
, pp. 2322-2324
-
-
Bellini, M.H.1
Peroni, C.N.2
Bartolini, P.3
-
16
-
-
12744280735
-
A review of gene therapy for haematological disorders
-
Nathwani, A. C., Davidoff, A. M., and Linch, D. C. (2004) A review of gene therapy for haematological disorders. B. J. Haematol. 128, 3-17.
-
(2004)
B. J. Haematol
, vol.128
, pp. 3-17
-
-
Nathwani, A.C.1
Davidoff, A.M.2
Linch, D.C.3
-
17
-
-
0035822005
-
Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A
-
Roth, D. A., Tawa, N. E., O'Brien, J. M., Treco, D. A., and Selden, R. F. (2001) Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A. N. Engl. J. Med. 344, 1735-1742.
-
(2001)
N. Engl. J. Med
, vol.344
, pp. 1735-1742
-
-
Roth, D.A.1
Tawa, N.E.2
O'Brien, J.M.3
Treco, D.A.4
Selden, R.F.5
-
18
-
-
2342514898
-
Clinical gene transfer studies for hemophilia A
-
Chuah, M. K. L., Collen, D., and VandenDriessche, T. (2004) Clinical gene transfer studies for hemophilia A. Semin.Thromb. Hemost. 30, 249-256.
-
(2004)
Semin.Thromb. Hemost
, vol.30
, pp. 249-256
-
-
Chuah, M.K.L.1
Collen, D.2
VandenDriessche, T.3
-
19
-
-
0032503628
-
Corrective transduction of human epidermal stem cells in laminin-5-dependent junctional epidermolysis bullosa
-
Dellambra, E., Vailly, J., Pellegrini, G., et al. (1998) Corrective transduction of human epidermal stem cells in laminin-5-dependent junctional epidermolysis bullosa. Hum. Gene Ther. 9, 1359-1370.
-
(1998)
Hum. Gene Ther
, vol.9
, pp. 1359-1370
-
-
Dellambra, E.1
Vailly, J.2
Pellegrini, G.3
-
20
-
-
0034330406
-
Toward epidermal stem cell-mediated ex vivo gene therapy of junctional epidermolysis bullosa
-
Dellambra, E., Pellegrini, G., Guerra, L., et al. (2000) Toward epidermal stem cell-mediated ex vivo gene therapy of junctional epidermolysis bullosa. Hum. Gene Ther. 11, 2283-2287.
-
(2000)
Hum. Gene Ther
, vol.11
, pp. 2283-2287
-
-
Dellambra, E.1
Pellegrini, G.2
Guerra, L.3
-
21
-
-
13544262329
-
Progress and prospects of skin gene therapy: A ten year history
-
Hengge, U. R. (2005) Progress and prospects of skin gene therapy: a ten year history. Clin. Dermatol. 23, 107-114.
-
(2005)
Clin. Dermatol
, vol.23
, pp. 107-114
-
-
Hengge, U.R.1
-
22
-
-
22044435548
-
Gene therapy for epidermolysis bullosa
-
Ferrari, S., Pellegrini, G., Mavilio, F., and De Luca, M. (2005) Gene therapy for epidermolysis bullosa. Clin. Dermatol. 23, 430-436.
-
(2005)
Clin. Dermatol
, vol.23
, pp. 430-436
-
-
Ferrari, S.1
Pellegrini, G.2
Mavilio, F.3
De Luca, M.4
-
23
-
-
0016728261
-
Formation of a keratinizing epithelium in culture by a cloned cell line derived from a teratoma
-
Rheinwald, J. G. and Green, H. (1975) Formation of a keratinizing epithelium in culture by a cloned cell line derived from a teratoma. Cell 6, 317-330.
-
(1975)
Cell
, vol.6
, pp. 317-330
-
-
Rheinwald, J.G.1
Green, H.2
-
24
-
-
0019351799
-
Grafting of burns with cultured epithelium prepared from autologous epidermal cells
-
O'Connor, N. E., Mulliken, J. B., Banks-Schlegel, S., Kehinde, O., and Green, H. (1981) Grafting of burns with cultured epithelium prepared from autologous epidermal cells. Lancet 1, 75-78.
-
(1981)
Lancet
, vol.1
, pp. 75-78
-
-
O'Connor, N.E.1
Mulliken, J.B.2
Banks-Schlegel, S.3
Kehinde, O.4
Green, H.5
-
25
-
-
0024427542
-
Multicentre experience in the treatment of burns with autologous and allogenic cultured epithelium, fresh or preserved in a frozen state
-
De Luca, M., Albanese, E., Bondanza, S., et al. (1989) Multicentre experience in the treatment of burns with autologous and allogenic cultured epithelium, fresh or preserved in a frozen state. Burns 15, 303-309.
-
(1989)
Burns
, vol.15
, pp. 303-309
-
-
De Luca, M.1
Albanese, E.2
Bondanza, S.3
-
26
-
-
0032213367
-
Cultivation of human keratinocyte stem cells: Current and future clinical applications
-
Pellegrini, G., Bondanza, S., Guerra, L., and De Luca, M. (1998) Cultivation of human keratinocyte stem cells: current and future clinical applications. Med. Biol. Eng. Comput. 36, 778-790.
-
(1998)
Med. Biol. Eng. Comput
, vol.36
, pp. 778-790
-
-
Pellegrini, G.1
Bondanza, S.2
Guerra, L.3
De Luca, M.4
-
28
-
-
0034332409
-
Regulated cutaneous gene delivery: The skin as a bioreactor
-
Cao, T., Wang, X., and Roop, D. R. (2000) Regulated cutaneous gene delivery: the skin as a bioreactor. Hum. Gene Ther. 11, 2297-2300.
-
(2000)
Hum. Gene Ther
, vol.11
, pp. 2297-2300
-
-
Cao, T.1
Wang, X.2
Roop, D.R.3
-
29
-
-
0032968687
-
Systemic replacement therapy from genetically modified epidermal keratinocytes
-
Taichman, L. B. (1999) Systemic replacement therapy from genetically modified epidermal keratinocytes. Proc. Assoc. Am. Physicians 111, 206-210.
-
(1999)
Proc. Assoc. Am. Physicians
, vol.111
, pp. 206-210
-
-
Taichman, L.B.1
-
30
-
-
0032918374
-
Persistent transgene expression and normal differentiation of immortalized human keratinocytes in vivo
-
Krueger, G. G., Jorgensen, C. M., Matsunami, N., et al. (1999) Persistent transgene expression and normal differentiation of immortalized human keratinocytes in vivo. J. Invest. Dermatol. 112, 233-239.
-
(1999)
J. Invest. Dermatol
, vol.112
, pp. 233-239
-
-
Krueger, G.G.1
Jorgensen, C.M.2
Matsunami, N.3
-
31
-
-
0023273993
-
Expression of an exogenous growth hormone gene by transplantable human epidermal cells
-
Morgan, J. R., Barrandon, Y., Green, H., and Mulligan, R. C. (1987) Expression of an exogenous growth hormone gene by transplantable human epidermal cells. Science 237, 1476-1479.
-
(1987)
Science
, vol.237
, pp. 1476-1479
-
-
Morgan, J.R.1
Barrandon, Y.2
Green, H.3
Mulligan, R.C.4
-
32
-
-
0025247075
-
Human growth hormone in the blood of athymic mice grafted with cultures of hormone-secreting human keratinocytes
-
Teumer, J., Lindahl, A., and Green, H. (1990) Human growth hormone in the blood of athymic mice grafted with cultures of hormone-secreting human keratinocytes. FASEB J. 4, 3245-3250.
-
(1990)
FASEB J
, vol.4
, pp. 3245-3250
-
-
Teumer, J.1
Lindahl, A.2
Green, H.3
-
33
-
-
0019471387
-
Tumorigenic keratinocyte lines requiring anchorage and fibroblast support cultured from human squamous cell carcinomas
-
Rheinwald, J. G. and Beckett, M. A. (1981) Tumorigenic keratinocyte lines requiring anchorage and fibroblast support cultured from human squamous cell carcinomas. Cancer Res. 41, 1657-1663.
-
(1981)
Cancer Res
, vol.41
, pp. 1657-1663
-
-
Rheinwald, J.G.1
Beckett, M.A.2
-
34
-
-
0028007366
-
Gene transfer into culture human epidermis and its transplantation onto immunodeficient mice: An experimental model for somatic gene therapy
-
Jensen, U. B., Jensen, T. G., Jensen, P. K. A., et al. (1994) Gene transfer into culture human epidermis and its transplantation onto immunodeficient mice: an experimental model for somatic gene therapy. J. Invest. Dermatol. 103, 391-394.
-
(1994)
J. Invest. Dermatol
, vol.103
, pp. 391-394
-
-
Jensen, U.B.1
Jensen, T.G.2
Jensen, P.K.A.3
-
35
-
-
0028095016
-
Genetically modified keratinocytes transplanted to wounds reconstitute the epidermis
-
Vogt, P. M., Thompson, S., Andree, C., et al. (1994) Genetically modified keratinocytes transplanted to wounds reconstitute the epidermis. Proc. Natl. Acad. Sci. USA 91, 9307-9311.
-
(1994)
Proc. Natl. Acad. Sci. USA
, vol.91
, pp. 9307-9311
-
-
Vogt, P.M.1
Thompson, S.2
Andree, C.3
-
36
-
-
0024460181
-
Improved retroviral vectors for gene transfer and expression
-
Miller, A. D. and Rosman, G. J. (1989) Improved retroviral vectors for gene transfer and expression. Biotechniques 7, 980-990.
-
(1989)
Biotechniques
, vol.7
, pp. 980-990
-
-
Miller, A.D.1
Rosman, G.J.2
-
37
-
-
0023814557
-
New techniques for the grafting of cultured human epidermal cells onto athymic animals
-
Barrandon, Y., Li, V., and Green, H. (1988) New techniques for the grafting of cultured human epidermal cells onto athymic animals. J. Invest. Dermatol. 91, 315-318.
-
(1988)
J. Invest. Dermatol
, vol.91
, pp. 315-318
-
-
Barrandon, Y.1
Li, V.2
Green, H.3
-
38
-
-
0028171601
-
Effect of TGF-β1 on re-epithelization of human keratinocytes in vitro: An organotypic model
-
Garlick, J. A. and Taichman, L. B. (1994) Effect of TGF-β1 on re-epithelization of human keratinocytes in vitro: an organotypic model. J. Invest. Dermatol. 103, 554-559.
-
(1994)
J. Invest. Dermatol
, vol.103
, pp. 554-559
-
-
Garlick, J.A.1
Taichman, L.B.2
-
39
-
-
0032516016
-
Evidence for keratinocyte stem cells in vitro: Long term engraftment and persistence of transgene expression from retrovirus-transduced keratinocytes
-
Kolodka, T. M., Garlick, J. A., and Taichman, L. B. (1998) Evidence for keratinocyte stem cells in vitro: long term engraftment and persistence of transgene expression from retrovirus-transduced keratinocytes. Proc. Natl. Acad. Sci. USA 95, 4356-4361.
-
(1998)
Proc. Natl. Acad. Sci. USA
, vol.95
, pp. 4356-4361
-
-
Kolodka, T.M.1
Garlick, J.A.2
Taichman, L.B.3
-
40
-
-
0035145339
-
Isolating a pure population of epidermal stem cells for use in tissue engineering
-
Dunnwald, M., Tomaneck-Chalkley, A., Alexandrunas, D., Fishbaugh, J., and Bickenbach, J. R. (2001) Isolating a pure population of epidermal stem cells for use in tissue engineering. Exp. Dermatol. 10, 45-54.
-
(2001)
Exp. Dermatol
, vol.10
, pp. 45-54
-
-
Dunnwald, M.1
Tomaneck-Chalkley, A.2
Alexandrunas, D.3
Fishbaugh, J.4
Bickenbach, J.R.5
-
41
-
-
19444363757
-
Efficient gene transfer to human epidermal keratinocytes on fibronectin: In vitro evidence for transduction of epidermal stem cells
-
Bajaj, B. G., Lei, P., and Andreadis, S. T. (2005) Efficient gene transfer to human epidermal keratinocytes on fibronectin: in vitro evidence for transduction of epidermal stem cells. Mol. Ther. 11, 969-979.
-
(2005)
Mol. Ther
, vol.11
, pp. 969-979
-
-
Bajaj, B.G.1
Lei, P.2
Andreadis, S.T.3
-
42
-
-
0029790151
-
Clonal analysis of stably transduced human epidermal stem cells in culture
-
Mathor, M. B., Ferrari, G., Dellambra, E., et al. (1996) Clonal analysis of stably transduced human epidermal stem cells in culture. Proc. Natl. Acad. Sci. USA 93, 10,371-10,376.
-
(1996)
Proc. Natl. Acad. Sci. USA
, vol.93
-
-
Mathor, M.B.1
Ferrari, G.2
Dellambra, E.3
-
43
-
-
0027465539
-
Towards gene therapy for haemophilia B using primary human keratinocytes
-
Gerrard, A. J., Hudson, D. L., Brownlee, G. G., and Watt, F. M. (1993) Towards gene therapy for haemophilia B using primary human keratinocytes. Nature Genet. 3, 180-183.
-
(1993)
Nature Genet
, vol.3
, pp. 180-183
-
-
Gerrard, A.J.1
Hudson, D.L.2
Brownlee, G.G.3
Watt, F.M.4
-
44
-
-
0029828128
-
Phenotypic correction of dwarfism by constitutive expression of growth hormone
-
Hahn, T. M., Copeland, K. C., and Woo, S. L. C. (1996) Phenotypic correction of dwarfism by constitutive expression of growth hormone. Endocrinology 137, 4988-4993.
-
(1996)
Endocrinology
, vol.137
, pp. 4988-4993
-
-
Hahn, T.M.1
Copeland, K.C.2
Woo, S.L.C.3
|