메뉴 건너뛰기




Volumn 38, Issue 3, 2006, Pages 171-176

Orphan diseases and drugs

Author keywords

Drugs for neglected diseases initiative; Neglected diseases; Orphan drugs

Indexed keywords

ALGLUCERASE; ALPHA 1 ANTITRYPSIN; AMINOPENICILLIN; ANTITHROMBIN III; ARTEMETHER; ARTESUNATE; BLOOD CLOTTING FACTOR 9; CARNITINE; CHOLECYSTOKININ OCTAPEPTIDE; FANSIDAR; FELBAMATE; HALOFANTRINE; HUMAN GROWTH HORMONE; IMIGLUCERASE; ISONIAZID; IVERMECTIN; LAMOTRIGINE; MEFLOQUINE; OCTREOTIDE; ORPHAN DRUG; PENICILLAMINE; RIFABUTIN; RIFAMPICIN; RIFAPENTINE; RILUZOLE; TETRATHIOMOLYBDATE AMMONIUM; THALIDOMIDE; TOPIRAMATE; TRANEXAMIC ACID; UNINDEXED DRUG;

EID: 33745161543     PISSN: 02537613     EISSN: None     Source Type: Journal    
DOI: 10.4103/0253-7613.25803     Document Type: Review
Times cited : (2)

References (33)
  • 1
    • 0036588777 scopus 로고    scopus 로고
    • Orphan drugs: Legal aspects, current situation
    • Lavandeira A. Orphan drugs: Legal aspects, current situation. Haemophilia 2002;8:194-8.
    • (2002) Haemophilia , vol.8 , pp. 194-198
    • Lavandeira, A.1
  • 2
    • 0035415511 scopus 로고    scopus 로고
    • Orphan drugs and orphan diseases
    • Campos-Castello J. Orphan drugs and orphan diseases. Rev Neurol 2001;33:216-20.
    • (2001) Rev Neurol , vol.33 , pp. 216-220
    • Campos-Castello, J.1
  • 4
    • 33745123128 scopus 로고    scopus 로고
    • How TV Launched the Orphan Drug Law
    • Henkel J. How TV Launched the Orphan Drug Law. FDA Consumer Magazine. Available from: http://www.fda.gov/fdac/features/1999/399_orph.html#tv
    • FDA Consumer Magazine
    • Henkel, J.1
  • 5
    • 0037157590 scopus 로고    scopus 로고
    • Drug development for neglected diseases: A deficient market and a public-health policy failure
    • Trouiller P, Olliaro P, Els Torreele, Orbinski J, Laing R, Ford N. Drug development for neglected diseases: A deficient market and a public-health policy failure. Lancet 2002;359:2188-94.
    • (2002) Lancet , vol.359 , pp. 2188-2194
    • Trouiller, P.1    Olliaro, P.2    Torreele, E.3    Orbinski, J.4    Laing, R.5    Ford, N.6
  • 7
    • 17344395558 scopus 로고    scopus 로고
    • Orphan drugs and metabolic disorders
    • 1-15
    • Martinez-Pardo M. Orphan drugs and metabolic disorders. Rev Neurol 2001 1-15; 33:220-5.
    • (2001) Rev Neurol , vol.33 , pp. 220-225
    • Martinez-Pardo, M.1
  • 8
    • 0025762252 scopus 로고
    • Orphan products: Origins, progress and prospects
    • Haffner M. Orphan products: Origins, progress and prospects. Annu Rev Pharmacol Toxicol 1991;31:603-20.
    • (1991) Annu Rev Pharmacol Toxicol , vol.31 , pp. 603-620
    • Haffner, M.1
  • 9
    • 0026448022 scopus 로고
    • Evaluation of orphan products by the US. Food and Drug Administration
    • Haffner M, Kelsey J. Evaluation of orphan products by the US. Food and Drug Administration. Int J Tech Assess Health Care 1992;8:647-57.
    • (1992) Int J Tech Assess Health Care , vol.8 , pp. 647-657
    • Haffner, M.1    Kelsey, J.2
  • 11
    • 1642547104 scopus 로고    scopus 로고
    • Developing treatments for inborn errors: Incentives available to the clinician
    • Haffner ME. Developing treatments for inborn errors: Incentives available to the clinician. Mol Genet Metab 2004;81:63-6.
    • (2004) Mol Genet Metab , vol.81 , pp. 63-66
    • Haffner, M.E.1
  • 12
    • 33749216944 scopus 로고    scopus 로고
    • Across-national comparison of orphan drug policies: Implications for the US Orphan Drug Act
    • Thamer M, Brennan N, Semansky R. Across-national comparison of orphan drug policies: implications for the US Orphan Drug Act. J Health Pol Policy Law 1998;23:265-90.
    • (1998) J Health Pol Policy Law , vol.23 , pp. 265-290
    • Thamer, M.1    Brennan, N.2    Semansky, R.3
  • 13
    • 33745170868 scopus 로고    scopus 로고
    • Published: 01 December 2001 Source: Frost & Sullivan
    • Ariely R. The Rise of Biopharmaceutical Orphan Drug Adoption. [Published: 01 December 2001 Source: Frost & Sullivan]. Available from: http://www.inpharm.com/intelligence/frost071201.html
    • The Rise of Biopharmaceutical Orphan Drug Adoption
    • Ariely, R.1
  • 14
    • 0033282751 scopus 로고    scopus 로고
    • Anecdotal therapies
    • Millikan LE. Anecdotal therapies. Adv Exp Med Biol 1999;455:407-11.
    • (1999) Adv Exp Med Biol , vol.455 , pp. 407-411
    • Millikan, L.E.1
  • 15
    • 13144272331 scopus 로고    scopus 로고
    • Food and Drug Administration. The Orphan Drug Act (as amended). [accessed 2002 May 6]. Available from: http://www.fda.gov/orphan/oda.htm
    • The Orphan Drug Act (As Amended)
  • 16
    • 0037337399 scopus 로고    scopus 로고
    • Treatment of Wilson disease with ammonium tetrathiomolybdate: III. Initial therapy in a total of 55 neurologically affected patients and follow-up with zinc therapy
    • Brewer GJ, Hedera P, Kluin KJ, Carlson M, Askari F, Dick RB, et al. Treatment of Wilson disease with ammonium tetrathiomolybdate: III. Initial therapy in a total of 55 neurologically affected patients and follow-up with zinc therapy. Arch Neurol 2003;60:379-85.
    • (2003) Arch Neurol , vol.60 , pp. 379-385
    • Brewer, G.J.1    Hedera, P.2    Kluin, K.J.3    Carlson, M.4    Askari, F.5    Dick, R.B.6
  • 17
    • 0033629558 scopus 로고    scopus 로고
    • Pharmaceutical development concerning diseases predominating in tropical regions: The concept of indigent drugs
    • Trouiller P, Rey JL, Bouscharain P. Pharmaceutical development concerning diseases predominating in tropical regions: the concept of indigent drugs. Ann Pharm Fr 2000;58:43-6.
    • (2000) Ann Pharm Fr , vol.58 , pp. 43-46
    • Trouiller, P.1    Rey, J.L.2    Bouscharain, P.3
  • 19
    • 0022392936 scopus 로고
    • Orphan drugs: The question of product liability
    • Scharf S. Orphan drugs: the question of product liability. Am J Law Med 1985;10:491-513.
    • (1985) Am J Law Med , vol.10 , pp. 491-513
    • Scharf, S.1
  • 21
    • 0035451088 scopus 로고    scopus 로고
    • What are today's orphaned vaccines?
    • Wilde H. What are today's orphaned vaccines? Clin Infect Dis 2001;33:648-50.
    • (2001) Clin Infect Dis , vol.33 , pp. 648-650
    • Wilde, H.1
  • 22
    • 33745159496 scopus 로고    scopus 로고
    • Humanitarian Use Devices
    • Medical Devices
    • Medical Devices. Humanitarian Use Devices. Final rule federal register, v. 61. 1996.
    • (1996) Final Rule Federal Register, V. 61
  • 23
    • 0036173643 scopus 로고    scopus 로고
    • Orphan drug product regulation-US
    • Haffner ME. Orphan drug product regulation-US. Int J Clin Pharmacol Ther 2002;40:84-8.
    • (2002) Int J Clin Pharmacol Ther , vol.40 , pp. 84-88
    • Haffner, M.E.1
  • 24
    • 0035960428 scopus 로고    scopus 로고
    • Safety and efficacy of imatinib (STI571) in metastatic gastrointestinal stromal tumors: A Phase I study
    • Van Oossterom AT, Judson I, Verweji J. Safety and efficacy of imatinib (STI571) in metastatic gastrointestinal stromal tumors: A Phase I study. Lancet 2001;358:1421-3.
    • (2001) Lancet , vol.358 , pp. 1421-1423
    • Van Oossterom, A.T.1    Judson, I.2    Verweji, J.3
  • 26
    • 0035073392 scopus 로고    scopus 로고
    • Effect of a selective Abl tyrosine kinase inhibitor, STI571, on in vitro growth of BCR-ABL-positive acute lymphoblastic leukemia cells
    • Kawaguchi Y, Jinnai I, Nagai K. Effect of a selective Abl tyrosine kinase inhibitor, STI571, on in vitro growth of BCR-ABL-positive acute lymphoblastic leukemia cells. Leukemia 2001;15:590-4.
    • (2001) Leukemia , vol.15 , pp. 590-594
    • Kawaguchi, Y.1    Jinnai, I.2    Nagai, K.3
  • 27
    • 0035963315 scopus 로고    scopus 로고
    • Tyrosine kinase inhibitor STI571 enhances thyroid cancer cell motile response to hepatocyte growth factor
    • Frasca F, Vigneri P, Vella V. Tyrosine kinase inhibitor STI571 enhances thyroid cancer cell motile response to hepatocyte growth factor. Oncogene 2001;20:3845-56.
    • (2001) Oncogene , vol.20 , pp. 3845-3856
    • Frasca, F.1    Vigneri, P.2    Vella, V.3
  • 28
    • 0034665138 scopus 로고    scopus 로고
    • Intracranial inhibition of platelet-derived growth factor-mediated glioblastoma cell growth by an orally active kinase inhibitor of the 2-phenylaminopyrimidine class
    • KilicT, Alberta JA, Zdunek PR. Intracranial inhibition of platelet-derived growth factor-mediated glioblastoma cell growth by an orally active kinase inhibitor of the 2-phenylaminopyrimidine class. Cancer Res 2000;60:5143-50.
    • (2000) Cancer Res , vol.60 , pp. 5143-5150
    • Kilic, T.1    Alberta, J.A.2    Zdunek, P.R.3
  • 29
    • 0033883653 scopus 로고    scopus 로고
    • The selective tyrosine kinase inhibitor STI571 inhibits small cell lung cancer growth
    • Krystal GW, Honsawek S, Litz J. The selective tyrosine kinase inhibitor STI571 inhibits small cell lung cancer growth. Clin Cancer Res 2000;6:3319-26.
    • (2000) Clin Cancer Res , vol.6 , pp. 3319-3326
    • Krystal, G.W.1    Honsawek, S.2    Litz, J.3
  • 30
    • 0038283055 scopus 로고    scopus 로고
    • Established by FDA to Expedite Patient Access to Medications
    • Motl S, Miller SJ, Burns P. Established by FDA to Expedite Patient Access to Medications. Am J Health-Syst Pharm 2003;60:339-45.
    • (2003) Am J Health-Syst Pharm , vol.60 , pp. 339-345
    • Motl, S.1    Miller, S.J.2    Burns, P.3
  • 31
    • 33344478177 scopus 로고    scopus 로고
    • New initiative to develop drugs for neglected diseases
    • Banerji J. New initiative to develop drugs for neglected diseases. Essential Drug Monitor 2003;33:28.
    • (2003) Essential Drug Monitor , vol.33 , pp. 28
    • Banerji, J.1
  • 32
    • 0038678846 scopus 로고    scopus 로고
    • Nuclear transplatation, embryonic stem cells, and the potential for cell therapy
    • Hochedlinger and Jaenisch. Nuclear transplatation, embryonic stem cells, and the potential for cell therapy. N Engl J Med 2003;349:275-86.
    • (2003) N Engl J Med , vol.349 , pp. 275-286
    • Hochedlinger1    Jaenisch2
  • 33
    • 33745124169 scopus 로고    scopus 로고
    • Nuclear transfer and therapeutic cloning
    • Xu XM, Lei AM, Hua JL, Dou ZY. Nuclear transfer and therapeutic cloning. Yi Chuan 2005;27:289-96.
    • (2005) Yi Chuan , vol.27 , pp. 289-296
    • Xu, X.M.1    Lei, A.M.2    Hua, J.L.3    Dou, Z.Y.4


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.