-
1
-
-
85120203623
-
Enhanced rescue of OTC deficiency using novel adeno-associated virus vectors
-
H. Morizono Enhanced rescue of OTC deficiency using novel adeno-associated virus vectors Mol. Genet. Metab. 84 2005 230 231
-
(2005)
Mol. Genet. Metab.
, vol.84
, pp. 230-231
-
-
Morizono, H.1
-
2
-
-
33745250487
-
Analysis of Tumors Arising in Male B6C3F1 Mice with and without AAV Vector Delivery to Liver
-
P. Bell Analysis of Tumors Arising in Male B6C3F1 Mice with and without AAV Vector Delivery to Liver Mol. Ther. 14 2006 34 45
-
(2006)
Mol. Ther.
, vol.14
, pp. 34-45
-
-
Bell, P.1
-
3
-
-
33745118671
-
Long-Term Correction of Ammonia Metabolism and Prolonged Survival in Ornithine Transcarbamylase-Deficient Mice Following Liver-Directed Treatment with Novel Adeno-associated Viral Vectors
-
D. Moscioni Long-Term Correction of Ammonia Metabolism and Prolonged Survival in Ornithine Transcarbamylase-Deficient Mice Following Liver-Directed Treatment with Novel Adeno-associated Viral Vectors Mol. Ther. 14 2006 25 33
-
(2006)
Mol. Ther.
, vol.14
, pp. 25-33
-
-
Moscioni, D.1
-
4
-
-
0032732091
-
Liver transplantation in urea cycle disorders
-
J.M. Saudubray Liver transplantation in urea cycle disorders Eur. J. Pediatr. 158 Suppl 2 1999 S55 S59
-
(1999)
Eur. J. Pediatr.
, vol.158
, Issue.Suppl 2
, pp. S55-S59
-
-
Saudubray, J.M.1
-
5
-
-
0031903608
-
Developing adenoviral-mediated in vivo gene therapy for ornithine transcarbamylase deficiency
-
S.E. Raper Developing adenoviral-mediated in vivo gene therapy for ornithine transcarbamylase deficiency J. Inherit. Metab. Dis. 21 Suppl 1 1998 119 137
-
(1998)
J. Inherit. Metab. Dis.
, vol.21
, Issue.Suppl 1
, pp. 119-137
-
-
Raper, S.E.1
-
6
-
-
0142089747
-
Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer
-
S.E. Raper Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer Mol. Genet. Metab. 80 2003 148 158
-
(2003)
Mol. Genet. Metab.
, vol.80
, pp. 148-158
-
-
Raper, S.E.1
-
7
-
-
0037015049
-
Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy
-
G.P. Gao Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy Proc. Natl. Acad. Sci. USA 99 2002 11854 11859
-
(2002)
Proc. Natl. Acad. Sci. USA
, vol.99
, pp. 11854-11859
-
-
Gao, G.P.1
-
8
-
-
0034830365
-
Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors
-
A. Donsante Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors Gene Ther. 8 2001 1343 1346
-
(2001)
Gene Ther.
, vol.8
, pp. 1343-1346
-
-
Donsante, A.1
-
9
-
-
32444436226
-
Long-term correction of murine glycogen storage disease type Ia by recombinant adeno-associated virus-1-mediated gene transfer
-
A. Ghosh Long-term correction of murine glycogen storage disease type Ia by recombinant adeno-associated virus-1-mediated gene transfer Gene Ther. 13 2006 321 329
-
(2006)
Gene Ther.
, vol.13
, pp. 321-329
-
-
Ghosh, A.1
-
10
-
-
33747600886
-
Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia
-
D.D. Koeberl Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia Gene Ther. 2006 Epub ahead of press.
-
(2006)
Gene Ther.
-
-
Koeberl, D.D.1
-
11
-
-
0026092941
-
Mutational activation of the c-Ha-ras gene in liver tumors of different rodent strains: correlation with susceptibility to hepatocarcinogenesis
-
A. Buchmann Mutational activation of the c-Ha-ras gene in liver tumors of different rodent strains: correlation with susceptibility to hepatocarcinogenesis Proc. Natl. Acad. Sci. USA 88 1991 911 915
-
(1991)
Proc. Natl. Acad. Sci. USA
, vol.88
, pp. 911-915
-
-
Buchmann, A.1
-
12
-
-
22644433751
-
No evidence for tumorigenesis of AAV vectors in a large-scale study in mice
-
P. Bell No evidence for tumorigenesis of AAV vectors in a large-scale study in mice Mol. Ther. 12 2005 299 306
-
(2005)
Mol. Ther.
, vol.12
, pp. 299-306
-
-
Bell, P.1
|